Effects of tofersen treatment in patients with SOD1-ALS in a "real-world" setting - a 12-month multicenter cohort study from the German early access program
在“真实世界”环境下,托福生治疗对SOD1-ALS患者的疗效——一项来自德国早期准入计划的为期12个月的多中心队列研究
期刊:EClinicalMedicine
影响因子:10
doi:10.1016/j.eclinm.2024.102495
Wiesenfarth, Maximilian; Dorst, Johannes; Brenner, David; Elmas, Zeynep; Parlak, Özlem; Uzelac, Zeljko; Kandler, Katharina; Mayer, Kristina; Weiland, Ulrike; Herrmann, Christine; Schuster, Joachim; Freischmidt, Axel; Müller, Kathrin; Siebert, Reiner; Bachhuber, Franziska; Simak, Tatiana; Günther, Kornelia; Fröhlich, Elke; Knehr, Antje; Regensburger, Martin; German, Alexander; Petri, Susanne; Grosskreutz, Julian; Klopstock, Thomas; Reilich, Peter; Schöberl, Florian; Hagenacker, Tim; Weyen, Ute; Günther, René; Vidovic, Maximilian; Jentsch, Martin; Haarmeier, Thomas; Weydt, Patrick; Valkadinov, Ivan; Hesebeck-Brinckmann, Jasper; Conrad, Julian; Weishaupt, Jochen Hans; Schumann, Peggy; Körtvélyessy, Peter; Meyer, Thomas; Ruf, Wolfgang Philipp; Witzel, Simon; Senel, Makbule; Tumani, Hayrettin; Ludolph, Albert Christian