Intra-CSF AAV9 and AAVrh10 Administration in Nonhuman Primates: Promising Routes and Vectors for Which Neurological Diseases?
在非人灵长类动物中脑脊液内注射 AAV9 和 AAVrh10:哪些神经系统疾病有前景的途径和载体?
期刊:Molecular Therapy-Methods & Clinical Development
影响因子:4.7
doi:10.1016/j.omtm.2020.04.001
Bey, Karim; Deniaud, Johan; Dubreil, Laurence; Joussemet, Béatrice; Cristini, Joseph; Ciron, Carine; Hordeaux, Juliette; Le Boulc'h, Morwenn; Marche, Kevin; Maquigneau, Maud; Guilbaud, Michaël; Moreau, Rosalie; Larcher, Thibaut; Deschamps, Jack-Yves; Fusellier, Marion; Blouin, Véronique; Sevin, Caroline; Cartier, Nathalie; Adjali, Oumeya; Aubourg, Patrick; Moullier, Philippe; Colle, Marie-Anne