Long-term mitapivat treatment is safe and efficacious in patients with sickle cell disease
长期服用米塔匹伐治疗对镰状细胞病患者安全有效。
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影响因子:
doi:10.1016/j.brci.2025.100014
Conrey, Anna; Asomaning, Nancy; Frey, Ingrid; Charles, Ruth Pierre; Lovins, Dianna; Xu, Julia Z; Mendez-Marti, Sebastian; Le, Kang; Kruah, Britney; Li, Quan; Dunkelberger, Emily; Cellmer, Troy; Yates, Amber; Wind-Rotolo, Megan; Huston, Chris; Jeffries, Neal; Eaton, William A; Thein, Swee Lay