日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Patient-Specific In Vivo Gene Editing to Treat a Rare Genetic Disease

利用患者特异性体内基因编辑技术治疗罕见遗传疾病

Musunuru, Kiran; Grandinette, Sarah A; Wang, Xiao; Hudson, Taylor R; Briseno, Kevin; Berry, Anne Marie; Hacker, Julia L; Hsu, Alvin; Silverstein, Rachel A; Hille, Logan T; Ogul, Aysel N; Robinson-Garvin, Nancy A; Small, Juliana C; McCague, Sarah; Burke, Samantha M; Wright, Christina M; Bick, Sarah; Indurthi, Venkata; Sharma, Shweta; Jepperson, Michael; Vakulskas, Christopher A; Collingwood, Michael; Keogh, Katie; Jacobi, Ashley; Sturgeon, Morgan; Brommel, Christian; Schmaljohn, Ellen; Kurgan, Gavin; Osborne, Thomas; Zhang, He; Kinney, Kyle; Rettig, Garrett; Barbosa, Christopher J; Semple, Sean C; Tam, Ying K; Lutz, Cathleen; George, Lindsey A; Kleinstiver, Benjamin P; Liu, David R; Ng, Kim; Kassim, Sadik H; Giannikopoulos, Petros; Alameh, Mohamad-Gabriel; Urnov, Fyodor D; Ahrens-Nicklas, Rebecca C

Histone methyltransferase PRDM9 promotes survival of drug-tolerant persister cells in glioblastoma.

组蛋白甲基转移酶PRDM9促进胶质母细胞瘤中耐药持续细胞的存活。

Joun George L, Kempe Emma G, Chen Brianna, Sterling Jayden R, Abbassi Ramzi H, Friess Dana, Singleton Matthew, Choudhury Chandra, Marian Oana C, du Preez W Daniel, Recasens Ariadna, Clark Teleri, Du Tian Y, Low Jason K K, Kim Hani, Yang Pengyi, Khor Jasmine, Hoque Monira, Indurthi Dinesh C, Kuchibhotla Mani, Palanisamy Ranjith, Jorgensen William T, Montgomery Andrew P, Baker Jennifer R, Higginbottom Sarah L, Tomaskovic-Crook Eva, Crook Jeremy M, Loo Lipin, Day Bryan W, Neely G Gregory, Guccione Ernesto, Johns Terrance G, Kassiou Michael, Feng Yuchen, Harris Lachlan, Don Anthony S, Munoz Lenka

Efficient nonviral integration of large transgenes into human T cells using Cas9-CLIPT.

利用 Cas9-CLIPT 将大型转基因高效非病毒整合到人类 T 细胞中

Tommasi Anna, Cappabianca Dan, Bugel Madison, Gimse Kirstan, Lund-Peterson Karl, Shrestha Hum, Arutyunov Denis, Williams James A, Police Seshidhar Reddy, Indurthi Venkata, Davis Sage Z, Murtaza Muhammed, Capitini Christian M, Saha Krishanu

Harnessing Protein Unfolding for Thermosensing: Structural Insights from TRPV3

利用蛋白质展开进行温度传感:来自 TRPV3 的结构见解

Mugo, Andrew Njagi; Indurthi, Dinesh; Chou, Ryan; Yadav, Gaya P; Wang, Liguo; Qin, Feng

CHRFAM7A diversifies human immune adaption through Ca2+ signalling and actin cytoskeleton reorganization

CHRFAM7A 通过 Ca2+ 信号传导和肌动蛋白细胞骨架重组实现人类免疫适应多样化

Kinga Szigeti, Ivanna Ihnatovych, Emily Notari, Ryu P Dorn, Ivan Maly, Muye He, Barbara Birkaya, Shreyas Prasad, Robin Schwartz Byrne, Dinesh C Indurthi, Erik Nimmer, Yuna Heo, Kolos Retfalvi, Lee Chaves, Norbert Sule, Wilma A Hofmann, Anthony Auerbach, Gregory Wilding, Yongho Bae, Jessica Reynolds

Conformational dynamics of a nicotinic receptor neurotransmitter site

尼古丁受体神经递质位点的构象动力学

Singh, Mrityunjay; Indurthi, Dinesh C; Mittal, Lovika; Auerbach, Anthony; Asthana, Shailendra

Cytochrome bd oxidase: an emerging anti-tubercular drug target

细胞色素bd氧化酶:一种新兴的抗结核药物靶点

Saha, Pallavi; Das, Samarpita; Indurthi, Harish K; Kumar, Rohit; Roy, Arnab; Kalia, Nitin Pal; Sharma, Deepak K

Agonist efficiency links binding and gating in a nicotinic receptor

激动剂的效率与尼古丁受体的结合和门控有关

Indurthi, Dinesh C; Auerbach, Anthony

Agonist efficiency from concentration-response curves: Structural implications and applications

从浓度-反应曲线评估激动剂效率:结构意义和应用

Indurthi, Dinesh C; Auerbach, Anthony

CHRFAM7A: A human specific fusion gene, accounts for the translational gap for cholinergic strategies in Alzheimer's disease

CHRFAM7A:一种人类特异性融合基因,解释了阿尔茨海默病中胆碱能策略的翻译差距

Kinga Szigeti, Ivanna Ihnatovych, Barbara Birkaya, Ziqiang Chen, Aya Ouf, Dinesh C Indurthi, Jonathan E Bard, Julien Kann, Alexandrea Adams, Lee Chaves, Norbert Sule, Joan S Reisch, Valory Pavlik, Ralph H B Benedict, Anthony Auerbach, Gregory Wilding