Efficient in vivo base editing via single adeno-associated viruses with size-optimized genomes encoding compact adenine base editors
通过具有大小优化基因组并编码紧凑型腺嘌呤碱基编辑器的单个腺相关病毒进行有效的体内碱基编辑
期刊:Nature Biomedical Engineering
影响因子:26.8
doi:10.1038/s41551-022-00911-4
Jessie R Davis, Xiao Wang, Isaac P Witte, Tony P Huang, Jonathan M Levy, Aditya Raguram, Samagya Banskota, Nabil G Seidah, Kiran Musunuru, David R Liu