Characterization of early disease status in treatment-naive male paediatric patients with Fabry disease enrolled in a randomized clinical trial
对参与一项随机临床试验的未经治疗的法布里病男性儿童患者早期疾病状态进行表征
期刊:PLoS One
影响因子:2.6
doi:10.1371/journal.pone.0124987
Wijburg, Frits A; Bénichou, Bernard; Bichet, Daniel G; Clarke, Lorne A; Dostalova, Gabriela; Fainboim, Alejandro; Fellgiebel, Andreas; Forcelini, Cassiano; An Haack, Kristina; Hopkin, Robert J; Mauer, Michael; Najafian, Behzad; Scott, C Ronald; Shankar, Suma P; Thurberg, Beth L; Tøndel, Camilla; Tylki-Szymańska, Anna; Ramaswami, Uma