Gene editing in hematopoietic stem cells by co-delivery of Cas9/sgRNA ribonucleoprotein and templates for homology-directed repair in 'all-in-one' lentivirus-derived nanoparticles.
通过在“一体化”慢病毒衍生的纳米颗粒中共同递送 Cas9/sgRNA 核糖核蛋白和同源定向修复模板,对造血干细胞进行基因编辑
期刊:Nucleic Acids Research
影响因子:13.1
doi:10.1093/nar/gkaf767
Andersen Sofie, Wolff Jonas Holst, Skov Thomas Wisbech, Janns Jacob Hørlück, Davis Luther John, Haldrup Jakob H, Haslund Didde, Revenfeld Anne Louise, Relkovic Dinko, Møller Bjarne K, Lund Jacob, Bak Rasmus O, Thomsen Emil Aagaard, Mikkelsen Jacob Giehm