日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Utility of peripheral blood testing for detection and surveillance of clonal hematopoiesis in predisposed individuals

外周血检测在易感人群克隆性造血的检测和监测中的应用

Attardi, Enrico; Gray, Nathan; Lewis, Sara; Boals, Michelle; Shaker, Passant; Kotmayer, Lili; Sahoo, Sushree S; Li, Peng; Andersen, Erica F; Zhao, Jian; Pizzo, Lucilla; Oved, Joseph H; Jesudas, Rohith; Reiss, Ulrike M; Sharma, Richa; Christakopoulos, Georgios E; Bhoopalan, Senthil Velan; Takemoto, Clifford M; Kennedy, Alyssa; Voso, Maria Teresa; Kang, Guolian; Wlodarski, Marcin W

FBXO11 suppression rewires an NPM1-centered interactome influencing the progression of myelodysplastic syndrome

FBXO11抑制重塑以NPM1为中心的相互作用组,从而影响骨髓增生异常综合征的进展。

Niederkorn, Madeline; Bezavada, Lavanya; Cotton, Anitria; Palmer, Lance E; Konada, Lahiri; Hall, Trent; Pagala, Vishwajeeth R; Zhai, Jinbin; Yuan, Zuo-Fei; Fu, Yingxue; Steele, Jacob A; Narina, Shilpa; Schild, Andrew; Wu, Chengzhou; Aminov, Sarah; Schieber, Michael; McGovern, Erin; Taylor, Aaron B; Gurbuxani, Sandeep; Xu, Peng; Ji, Peng; Janke, Laura J; High, Anthony A; Kang, Guolian; Pruett-Miller, Shondra M; Weiss, Mitchell; Verma, Amit; Rampal, Raajit K; Crispino, John D

Increased Endothelin-1 and High-Risk APOL1 Variants Contribute to Albuminuria in Pediatric and Young Adults with Sickle Cell Anemia

内皮素-1 水平升高和高危 APOL1 变异体是镰状细胞贫血症患儿和青少年出现蛋白尿的原因。

Kasztan, Malgorzata; Kang, Guolian; Botta, Davide; Pollock, David M; Rashkin, Sara; Zahr, Rima; Lebensburger, Jeffrey

Sustained Clinical Benefit of AAV Gene Therapy in Severe Hemophilia B

AAV基因疗法在重度B型血友病中持续发挥临床疗效

Reiss, Ulrike M; Davidoff, Andrew M; Tuddenham, Edward G D; Chowdary, Pratima; McIntosh, Jenny; Muczynski, Vincent; Journou, Malo; Simini, Giulia; Ireland, Lydia; Mohamed, Saira; Riddell, Anne; Pie, Arnulfo J; Hall, Andrew; Quaglia, Alberto; Mangles, Sarah; Mahlangu, Johnny; Haley, Kristina; Recht, Michael; Shen, Yu-Min; Halka, Kathleen G; Fortner, Gail; Morton, Christopher L; Gu, Zhengming; Hayden, Randall T; Neufeld, Ellis J; Okhomina, Victoria I; Kang, Guolian; Nathwani, Amit C

Phase 3 randomized trial of high-dose methotrexate for young children with high-risk embryonal brain tumors: A report from the Children's Oncology Group

儿童肿瘤协作组关于高危胚胎性脑肿瘤患儿接受高剂量甲氨蝶呤治疗的3期随机试验报告

Mazewski, Claire; Leary, Sarah E S; Kang, Guolian; Li, Bryan K; Kellie, Stewart; Hayes, Laura; Shaw, Dennis; Ho, Ben; Reddy, Alyssa; Gossett, Jeffrey; Burger, Peter C; Judkins, Alexander R; Aridgides, Paul; Geyer, J Russell; Gajjar, Amar; Pollack, Ian F; Fouladi, Maryam; Huang, Annie

Age-dependent phenotypic and molecular evolution of pediatric MDS arising from GATA2 deficiency

GATA2缺陷引起的儿童MDS的年龄依赖性表型和分子演变

Kotmayer, Lili; Kozyra, Emilia J; Kang, Guolian; Strahm, Brigitte; Yoshimi, Ayami; Sahoo, Sushree S; Pastor, Victor B; Attardi, Enrico; Voss, Rebecca; Vinci, Luca; Kaiser, Max; Dworzak, Michael N; De Moerloose, Barbara; Sukova, Martina; Starý, Jan; Hasle, Henrik; Jahnukainen, Kirsi; Polychronopoulou, Sophia; Kállay, Krisztián; Smith, Owen P; Malone, Andrea; Barzilai Birenboim, Shlomit; Masetti, Riccardo; Buechner, Jochen; Ussowicz, Marek; Kjöllerström, Paula; Bodova, Ivana; Kavcic, Marko; Català, Albert; Turkiewicz, Dominik; Schmugge, Markus; de Haas, Valerie; Okhomina, Victoria I; Sotomayor, Cristian; Catalán, Paula; Wehr, Claudia; Salzer, Ulrich; Germing, Ulrich; Gattermann, Norbert; Bödör, Csaba; Gray, Nathan; Lewis, Sara; Shimamura, Akiko; Giorgetti, Alessandra; Erlacher, Miriam; Niemeyer, Charlotte M; Wlodarski, Marcin W

Development of Polygenic Risk Score for Persistent Albuminuria in Children and Adults With Sickle Cell Anemia

镰状细胞贫血症儿童和成人持续性蛋白尿多基因风险评分的开发

Zahr, Rima S; Kang, Guolian; Zhang, Xu; Rashkin, Sara R; Kovesdy, Csaba P; Takemoto, Clifford; Weiss, Mitch; Lebensburger, Jeffrey; Ataga, Kenneth I; Saraf, Santosh L

BCL11A-deficient human erythropoiesis is impaired in vitro and after xenotransplantation into mice.

BCL11A 缺陷的人类红细胞生成在体外和异种移植到小鼠后均受到损害

Jang Yoonjeong, Feng Ruopeng, Palmer Lance E, Mayuranathan Thiyagaraj, Yao Yu, Mayberry Kalin, Zhou Sheng, Xu Jian, Gossett Jeffrey M, Kang Guolian, Cheng Yong, Yen Jonathan S, Weiss Mitchell J

A Novel One-Sample Mendelian Randomization Approach for Count-Type Outcomes That Is Robust to Correlated and Uncorrelated Pleiotropic Effects

一种针对计数型结果的新型单样本孟德尔随机化方法,该方法对相关和非相关多效性效应均具有鲁棒性。

Liyanage, Janaka S S; Hankins, Jane S; Estepp, Jeremie H; Srivastava, Deokumar; Rashkin, Sara R; Takemoto, Clifford; Li, Yun; Cui, Yuehua; Mori, Motomi; Weiss, Mitchell J; Kang, Guolian

Hydroxyurea Therapy and Sleep-Disordered Breathing in Children With Sickle Cell Disease

羟基脲疗法与镰状细胞病患儿的睡眠呼吸障碍

Abramson, Zachary; Olanrewaju, Ayobami; Kang, Guolian; Olufadi, Yunusa; Chen, Pei-Lin; Rai, Parul; Heitzer, Andrew M; Takemoto, Clifford M; Bashir, Ahsan; Akil, Nour; Hankins, Jane S