日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

CRISPR/Cas9 gene therapy increases the risk of tumorigenesis in the mouse model of hereditary tyrosinemia type I.

CRISPR/Cas9 基因疗法增加了 I 型遗传性酪氨酸血症小鼠模型发生肿瘤的风险

Chen Tong, Barzi Mercedes, Furey Nika, Kim Hyunjae R, Pankowicz Francis P, Legras Xavier, Elsea Sara H, Hurley Ayrea E, Yang Diane, Wheeler David A, Borowiak Malgorzata, Bissig-Choisat Beatrice, Sumazin Pavel, Bissig Karl-Dimiter

Dissecting the effect of mitochondrial BCAT inhibition in methylmalonic acidemia.

剖析线粒体 BCAT 抑制对甲基丙二酸血症的影响。

Hemmingsen Madeline G, Zhang Guo-Fang, Ma Yunhan, Marchuk Hannah, Patel Kalyani R, Chen Tong, Li Xinning, Chapman Mark, Collias Sabrina, Lopez-Terrada Dolores H, Beasley James, Stiles Ashlee R, Chandler Randy J, Venditti Charles P, Young Sarah P, Barzi Mercedes, Bissig-Choisat Beatrice, Krafte Doug, Newgard Christopher B, Bissig Karl-Dimiter

High-potency MyoAAV capsids enhanced skeletal muscle correction in a mouse model of GSD IIIa

高活性MyoAAV衣壳增强了GSD IIIa小鼠模型的骨骼肌矫正效果

Liao, Kuo-An; Han, Sang-Oh; Barzi, Mercedes; Yi, Haiqing; Eisner, William; Bissig-Choisat, Beatrice; Bissig, Karl-Dimiter; Sun, Baodong

Circadian dysfunction induces NAFLD-related human liver cancer in a mouse model

昼夜节律紊乱在小鼠模型中诱发非酒精性脂肪性肝病相关的人类肝癌

Padilla, Jennifer; Osman, Noha M; Bissig-Choisat, Beatrice; Grimm, Sandra L; Qin, Xuan; Major, Angela M; Yang, Li; Lopez-Terrada, Dolores; Coarfa, Cristian; Li, Feng; Bissig, Karl-Dimiter; Moore, David D; Fu, Loning

A humanized mouse model for adeno-associated viral gene therapy

用于腺相关病毒基因治疗的人源化小鼠模型

Mercedes Barzi # ,Tong Chen # ,Trevor J Gonzalez ,Francis P Pankowicz ,Seh Hoon Oh ,Helen L Streff ,Alan Rosales ,Yunhan Ma ,Sabrina Collias ,Sarah E Woodfield ,Anna Mae Diehl ,Sanjeev A Vasudevan ,Thao N Galvan ,John Goss ,Charles A Gersbach ,Beatrice Bissig-Choisat ,Aravind Asokan ,Karl-Dimiter Bissig

Ex vivo gene editing and cell therapy for hereditary tyrosinemia type 1

体外基因编辑和细胞疗法治疗1型遗传性酪氨酸血症

Ates, Ilayda; Stuart, Callie; Rathbone, Tanner; Barzi, Mercedes; He, Gordon; Major, Angela M; Shankar, Vijay; Lyman, Rachel A; Angner, Sidney S; Mackay, Trudy F C; Srinivasan, Shanthi; Farris, Alton Brad; Bissig, Karl-Dimiter; Cottle, Renee N

Rescue of glutaric aciduria type I in mice by liver-directed therapies

通过肝脏靶向疗法挽救小鼠戊二酸尿症 I 型

Mercedes Barzi ,Collin G Johnson ,Tong Chen ,Ramona M Rodriguiz ,Madeline Hemmingsen ,Trevor J Gonzalez ,Alan Rosales ,James Beasley ,Cheryl K Peck ,Yunhan Ma ,Ashlee R Stiles ,Timothy C Wood ,Raquel Maeso-Diaz ,Anna Mae Diehl ,Sarah P Young ,Jeffrey I Everitt ,William C Wetsel ,William R Lagor ,Beatrice Bissig-Choisat ,Aravind Asokan ,Areeg El-Gharbawy ,Karl-Dimiter Bissig

The roles of Cyp1a2 and Cyp2d in pharmacokinetic profiles of serotonin and norepinephrine reuptake inhibitor duloxetine and its metabolites in mice

Cyp1a2 和 Cyp2d 在小鼠血清素和去甲肾上腺素再摄取抑制剂度洛西汀及其代谢物的药代动力学特征中的作用

Xuan Qin, Cen Xie, John M Hakenjos, Kevin R MacKenzie, Shelton R Boyd, Mercedes Barzi, Karl-Dimiter Bissig, Damian W Young, Feng Li

A hepatitis B virus transgenic mouse model with a conditional, recombinant, episomal genome

一种具有条件性重组游离基因组的乙型肝炎病毒转基因小鼠模型

Kruse, Robert L; Barzi, Mercedes; Legras, Xavier; Pankowicz, Francis P; Furey, Nika; Liao, Lan; Xu, Janming; Bissig-Choisat, Beatrice; Slagle, Betty L; Bissig, Karl-Dimiter

A human liver chimeric mouse model for non-alcoholic fatty liver disease

用于研究非酒精性脂肪肝疾病的人类肝脏嵌合小鼠模型

Bissig-Choisat, Beatrice; Alves-Bezerra, Michele; Zorman, Barry; Ochsner, Scott A; Barzi, Mercedes; Legras, Xavier; Yang, Diane; Borowiak, Malgorzata; Dean, Adam M; York, Robert B; Galvan, N Thao N; Goss, John; Lagor, William R; Moore, David D; Cohen, David E; McKenna, Neil J; Sumazin, Pavel; Bissig, Karl-Dimiter