Large-scale drug screening in iPSC-derived motor neurons from sporadic ALS patients identifies a potential combinatorial therapy
对散发性ALS患者诱导多能干细胞衍生的运动神经元进行大规模药物筛选,发现了一种潜在的联合疗法
期刊:Nature Neuroscience
影响因子:20
doi:10.1038/s41593-025-02118-7
Bye, Christopher R; Qian, Elizabeth; Lim, Katherine; Daniszewski, Maciej; Garton, Fleur C; Trần-Lê, Bảo C; Liang, Helena H; Lin, Tian; Lock, John G; Crombie, Duncan E; Morgan, Steven; Hu, Yi; Barton, Samantha K; Palmer, Lucy M; Djouma, Elvan; Kodikara, Saritha; Lê Cao, Kim-Anh; Dharmadasa, Thanuja; Henders, Anjali K; Ziser, Laura A; Kiernan, Matthew C; Talbot, Kevin; Needham, Merrilee; Fletcher, Susan; Talman, Paul; Mathers, Susan; Wray, Naomi R; Hewitt, Alex W; Pebay, Alice; Turner, Bradley J