In utero and postnatal ivacaftor/lumacaftor therapy rescues multiorgan disease in CFTR-F508del ferrets
宫内和出生后的ivacaftor/lumacaftor治疗可挽救CFTR-F508del雪貂的多器官疾病
期刊:JCI Insight
影响因子:6.3
doi:10.1172/jci.insight.157229
Idil Apak Evans, Xingshen Sun, Bo Liang, Amber R Vegter, Lydia Guo, Thomas J Lynch, Yan Zhang, Yulong Zhang, Yaling Yi, Yu Yang, Zehua Feng, Soo Yeun Park, Amanita Shonka, Hannah McCumber, Lisi Qi, Peipei Wu, Guangming Liu, Allison Lacina, Kai Wang, Katherine N Gibson-Corley, David K Meyerholz, Domi