日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Artificial intelligence-guided design of lipid nanoparticles for pulmonary gene therapy.

人工智能指导的脂质纳米颗粒设计用于肺部基因治疗

Witten Jacob, Raji Idris, Manan Rajith S, Beyer Emily, Bartlett Sandra, Tang Yinghua, Ebadi Mehrnoosh, Lei Junying, Nguyen Dien, Oladimeji Favour, Jiang Allen Yujie, MacDonald Elise, Hu Yizong, Mughal Haseeb, Self Ava, Collins Evan, Yan Ziying, Engelhardt John F, Langer Robert, Anderson Daniel G

Durable transgene expression and efficient re-administration after rAAV2.5T-mediated fCFTRΔR gene delivery to adult ferret lungs

rAAV2.5T介导的fCFTRΔR基因递送至成年雪貂肺部后,转基因表达持久且可有效重复给药

Tang, Yinghua; Ebadi, Mehrnoosh; Lei, Junying; Feng, Zehua; Fakhari, Shahab; Wu, Peipei; Smith, Mark D; Limberis, Maria P; Kolbeck, Roland; Excoffon, Katherine J; Yan, Ziying; Engelhardt, John F