Real-world outcomes of Voretigene Neparvovec: a single-centre consecutive case series
Voretigene Neparvovec 的真实世界疗效:单中心连续病例系列研究
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doi:10.1038/s41433-025-03637-0
Jalil, Assad; Ferrara, Mariantonia; Lippera, Myrta; Parry, Neil; Black, Graeme C; Banderas, Sandra; Ashworth, Jane; Biswas, Sus; Hall, Georgina; Gray, Jane; Newman, William; Ivanova, Tsveta