日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Genome-wide screening in pluripotent cells identifies Mtf1 as a suppressor of mutant huntingtin toxicity

全基因组筛选在多能干细胞中发现Mtf1是突变亨廷顿蛋白毒性的抑制因子

Giorgia Maria Ferlazzo #,Anna Maria Gambetta #,Sonia Amato #,Noemi Cannizzaro,Silvia Angiolillo,Mattia Arboit,Linda Diamante,Elena Carbognin,Patrizia Romani,Federico La Torre,Elena Galimberti,Florian Pflug,Mirko Luoni,Serena Giannelli,Giuseppe Pepe,Luca Capocci,Alba Di Pardo,Paola Vanzani,Lucio Zennaro,Vania Broccoli,Martin Leeb,Enrico Moro,Vittorio Maglione,Graziano Martello

Treatment with THI, an inhibitor of sphingosine-1-phosphate lyase, modulates glycosphingolipid metabolism and results therapeutically effective in experimental models of Huntington's disease

使用 THI(一种鞘氨醇-1-磷酸裂解酶抑制剂)进行治疗,可以调节糖鞘脂代谢,对亨廷顿氏病的实验模型具有治疗效果

Giuseppe Pepe, Luca Capocci, Federico Marracino, Natalia Realini, Paola Lenzi, Katiuscia Martinello, Tiziana Francesca Bovier, Terry Jo Bichell, Pamela Scarselli, Clotilde Di Cicco, Aaron B Bowman, Filomena A Digilio, Sergio Fucile, Francesco Fornai, Andrea Armirotti, Rosanna Parlato, Alba Di Pardo,

Blood-Brain Barrier Integrity Is Perturbed in a Mecp2-Null Mouse Model of Rett Syndrome

雷特综合征的 Mecp2 基因缺失小鼠模型中血脑屏障完整性受到干扰

Giuseppe Pepe, Salvatore Fioriniello, Federico Marracino, Luca Capocci, Vittorio Maglione, Maurizio D'Esposito, Alba Di Pardo, Floriana Della Ragione

Treatment with the Glycosphingolipid Modulator THI Rescues Myelin Integrity in the Striatum of R6/2 HD Mice

使用糖鞘脂调节剂 THI 治疗可挽救 R6/2 HD 小鼠纹状体中的髓鞘完整性

Giuseppe Pepe, Paola Lenzi, Luca Capocci, Federico Marracino, Ludovica Pizzati, Pamela Scarselli, Alba Di Pardo, Francesco Fornai, Vittorio Maglione

Polysialic Acid Sustains the Hypoxia-Induced Migration and Undifferentiated State of Human Glioblastoma Cells

聚唾液酸维持缺氧诱导的人类胶质母细胞瘤细胞迁移和未分化状态

Paolo Rosa, Sofia Scibetta, Giuseppe Pepe, Giorgio Mangino, Luca Capocci, Sam J Moons, Thomas J Boltje, Francesco Fazi, Vincenzo Petrozza, Alba Di Pardo, Vittorio Maglione, Antonella Calogero

Brain Region and Cell Compartment Dependent Regulation of Electron Transport System Components in Huntington's Disease Model Mice

亨廷顿氏病模型小鼠的脑区和细胞区室依赖性电子传输系统成分调节

Johannes Burtscher, Giuseppe Pepe, Federico Marracino, Luca Capocci, Susy Giova, Grégoire P Millet, Alba Di Pardo, Vittorio Maglione

Stimulation of Sphingosine Kinase 1 (SPHK1) Is Beneficial in a Huntington's Disease Pre-clinical Model

刺激鞘氨醇激酶 1 (SPHK1) 对亨廷顿氏病临床前模型有益

Alba Di Pardo, Giuseppe Pepe, Salvatore Castaldo, Federico Marracino, Luca Capocci, Enrico Amico, Michele Madonna, Susy Giova, Se Kyoo Jeong, Bu-Mahn Park, Byeong Deog Park, Vittorio Maglione