Ex vivo gene editing and cell therapy for hereditary tyrosinemia type 1
体外基因编辑和细胞疗法治疗1型遗传性酪氨酸血症
期刊:Hepatology Communications
影响因子:4.6
doi:10.1097/HC9.0000000000000424
Ates, Ilayda; Stuart, Callie; Rathbone, Tanner; Barzi, Mercedes; He, Gordon; Major, Angela M; Shankar, Vijay; Lyman, Rachel A; Angner, Sidney S; Mackay, Trudy F C; Srinivasan, Shanthi; Farris, Alton Brad; Bissig, Karl-Dimiter; Cottle, Renee N