SMN2 splice modulators enhance U1-pre-mRNA association and rescue SMA mice
SMN2 剪接调节剂增强 U1-pre-mRNA 结合并拯救 SMA 小鼠
期刊:Nature Chemical Biology
影响因子:12.9
doi:10.1038/nchembio.1837
James Palacino, Susanne E Swalley, Cheng Song, Atwood K Cheung, Lei Shu, Xiaolu Zhang, Mailin Van Hoosear, Youngah Shin, Donovan N Chin, Caroline Gubser Keller, Martin Beibel, Nicole A Renaud, Thomas M Smith, Michael Salcius, Xiaoying Shi, Marc Hild, Rebecca Servais, Monish Jain, Lin Deng, Caroline