Protracted CLN3 Batten disease in mice that genetically model an exon-skipping therapeutic approach
小鼠中长期 CLN3 巴顿病的遗传模型为外显子跳跃治疗方法
期刊:Molecular Therapy-Nucleic Acids
影响因子:6.5
doi:10.1016/j.omtn.2023.05.025
Jessica L Centa, Matthew P Stratton, Melissa A Pratt, Jenna R Osterlund Oltmanns, Douglas G Wallace, Steven A Miller, Jill M Weimer, Michelle L Hastings
