日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

A dual-fluorescence assay for gene delivery vehicle screening in macrophages with an inflammation-inducible reporter construct

一种用于巨噬细胞中基因递送载体筛选的双荧光检测方法,该方法使用炎症诱导型报告基因构建体。

Ivy, Allie; Bess, Shelby N; Agrawal, Shilpi; Kochar, Varun; Stokes, Abbey L; Muldoon, Timothy J; Nelson, Christopher E

Beyond the Cut: Long-read sequencing reveals complex genomic and transcriptomic changes in AAV-CRISPR therapy for Duchenne Muscular Dystrophy.

超越切割:长读测序揭示了 AAV-CRISPR 疗法治疗杜氏肌营养不良症中复杂的基因组和转录组变化

Jia Mary S, Padmaswari Made Harumi, Burcham Landon A, Agrawal Shilpi, Bulliard Gabrielle N, Stokes Abbey L, Nelson Christopher E

Standardizing a Protocol for Streamlined Synthesis and Characterization of Lipid Nanoparticles to Enable Preclinical Research and Education.

制定简化脂质纳米颗粒合成和表征的标准化方案,以促进临床前研究和教育

Agrawal Shilpi, Stokes Abbey L, Nelson Christopher E

PINE-TREE enables efficient enrichment of prime-edited hPSCs

PINE-TREE能够高效富集经基因编辑的hPSCs

Jia, Mary S; Nelson, Christopher E

Delivery challenges for CRISPR-Cas9 genome editing for Duchenne muscular dystrophy

CRISPR-Cas9基因编辑技术在杜氏肌营养不良症治疗中的递送挑战

Padmaswari, Made Harumi; Agrawal, Shilpi; Jia, Mary S; Ivy, Allie; Maxenberger, Daniel A; Burcham, Landon A; Nelson, Christopher E

In vivo genome editing improves muscle function in a mouse model of Duchenne muscular dystrophy

体内基因组编辑改善杜氏肌营养不良症小鼠模型的肌肉功能

Nelson, Christopher E; Hakim, Chady H; Ousterout, David G; Thakore, Pratiksha I; Moreb, Eirik A; Castellanos Rivera, Ruth M; Madhavan, Sarina; Pan, Xiufang; Ran, F Ann; Yan, Winston X; Asokan, Aravind; Zhang, Feng; Duan, Dongsheng; Gersbach, Charles A

Local Delivery of PHD2 siRNA from ROS-Degradable Scaffolds to Promote Diabetic Wound Healing

利用ROS可降解支架局部递送PHD2 siRNA促进糖尿病伤口愈合

Martin, John R; Nelson, Christopher E; Gupta, Mukesh K; Yu, Fang; Sarett, Samantha M; Hocking, Kyle M; Pollins, Alonda C; Nanney, Lillian B; Davidson, Jeffrey M; Guelcher, Scott A; Duvall, Craig L

Hydrolytic charge-reversal of PEGylated polyplexes enhances intracellular un-packaging and activity of siRNA

聚乙二醇化聚合物复合物的水解电荷反转可增强siRNA的细胞内解包装和活性。

Werfel, Thomas A; Swain, Corban; Nelson, Christopher E; Kilchrist, Kameron V; Evans, Brian C; Miteva, Martina; Duvall, Craig L

Technologies for controlled, local delivery of siRNA

用于控制局部递送siRNA的技术

Sarett, Samantha M; Nelson, Christopher E; Duvall, Craig L

Enhanced Performance of Plasmid DNA Polyplexes Stabilized by a Combination of Core Hydrophobicity and Surface PEGylation

核心疏水性和表面聚乙二醇化相结合可增强质粒DNA多聚体的性能

Adolph, Elizabeth J; Nelson, Christopher E; Werfel, Thomas A; Guo, Ruijing; Davidson, Jeffrey M; Guelcher, Scott A; Duvall, Craig L