In vivo genome editing improves muscle function in a mouse model of Duchenne muscular dystrophy
体内基因组编辑改善杜氏肌营养不良症小鼠模型的肌肉功能
期刊:Science
影响因子:45.8
doi:10.1126/science.aad5143
Nelson, Christopher E; Hakim, Chady H; Ousterout, David G; Thakore, Pratiksha I; Moreb, Eirik A; Castellanos Rivera, Ruth M; Madhavan, Sarina; Pan, Xiufang; Ran, F Ann; Yan, Winston X; Asokan, Aravind; Zhang, Feng; Duan, Dongsheng; Gersbach, Charles A