Use of CD19-targeted immune modulation to eradicate AAV-neutralizing antibodies.
利用 CD19 靶向免疫调节来根除 AAV 中和抗体
期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2025.03.003
Doshi Bhavya S, Markmann Caroline A, Novak Noelle, Juarez Rojas Silvia, Davidson Robert, Chau Julia Q, Wang Wei, Carrig Sean, Martos Rus Cristina, Samelson-Jones Benjamin J, Small Juliana C, Bhoj Vijay G, George Lindsey A