日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Intrathecal onasemnogene abeparvovec in treatment-naive patients with spinal muscular atrophy: a phase 3, randomized controlled trial

鞘内注射onasemnogene abeparvovec治疗初治脊髓性肌萎缩症患者:一项3期随机对照试验

Proud, Crystal M; Vũ, Dũng Chí; Wilmshurst, Jo M; Sanmaneechai, Oranee; Gulati, Sheffali; Xiong, Hui; Moreno, Hugo C; Tay, Stacey Kiat Hong; Thong, Meow-Keong; Born, Alfred Peter; Banzzatto Ortega, Adriana; Jong, Yuh-Jyh; Al-Muhaizea, Mohammad A; Lee, Anna W; Visootsak, Jeannie; Tauscher-Wisniewski, Sitra; Alecu, Iulian; Parlikar, Rutvick; Finkel, Richard S

Expanding the Genetic Landscape of Congenital Insensitivity to Pain

拓展先天性痛觉缺失的遗传图谱

Pho-Iam, Theeraphong; Kulsirichawaroj, Pimchanok; Likasitwattanakul, Surachai; Ridchuayrod, Numpueng; Sanmaneechai, Oranee; Limwongse, Chanin; Zuchner, Stephan

Enhanced sensitivity of lateral flow assay for NGAL detection using cysteamine-modified gold nanoparticles

利用半胱胺修饰的金纳米粒子提高侧向流动检测法对NGAL的灵敏度

Tunakhun, Paweena; Ngernpimai, Sawinee; Tippayawat, Patcharaporn; Choowongkomon, Kiattawee; Anutrakulchai, Sirirat; Charoensri, Nicha; Tavichakorntrakool, Ratree; Daduang, Sakda; Srichaiyapol, Oranee; Maraming, Pornsuda; Prompipak, Jeerati; Boonsiri, Patcharee; Daduang, Jureerut

Onasemnogene Abeparvovec Gene Therapy and Risdiplam for the Treatment of Spinal Muscular Atrophy in Thailand: A Cost-Utility Analysis

Onasemnogene Abeparvovec 基因疗法和 Risdiplam 用于治疗泰国脊髓性肌萎缩症:一项成本效益分析

Khuntha, Sarayuth; Prawjaeng, Juthamas; Ponragdee, Kunnatee; Sanmaneechai, Oranee; Srinonprasert, Varalak; Leelahavarong, Pattara

Validation and Reliability of the Thai Pediatric Charcot-Marie-Tooth Quality of Life Outcome Measure

泰国儿童夏科-马里-图斯病生活质量结局指标的验证和信度

Kulsirichawaroj, Pimchanok; Phochaisarn, Arisa; Limpaninlachat, Sivaporn; Vorasan, Nutchavadee; Likasitwattanakul, Surachai; Ramchandren, Sindhu; Shy, Michael E; Sanmaneechai, Oranee

Next-generation sequencing for pediatric-onset neuromuscular disorders unresolved by conventional diagnostic methods

针对传统诊断方法无法确诊的儿童期发病神经肌肉疾病,采用下一代测序技术进行诊断

Kulsirichawaroj, Pimchanok; Chanvanichtrakool, Mongkol; Wattanadilokchatkun, Pish; Pho-Iam, Theeraphong; Limwongse, Chanin; Likasitwattanakul, Surachai; Boonyapisit, Kanokwan; Sanmaneechai, Oranee; Nishino, Ichizo; Shotelersuk, Vorasuk; Han, Joohyun; Zuchner, Stephan

A Highly Sensitive Lateral-Flow Strip Using Latex Microspheres to Detect NGAL in Urine Samples

使用乳胶微球的高灵敏度横流试纸条检测尿液样本中的 NGAL

Paweena Tunakhun, Sawinee Ngernpimai, Patcharaporn Tippayawat, Kiattawee Choowongkomon, Sirirat Anutrakulchai, Nicha Charoensri, Ratree Tavichakorntrakool, Sakda Daduang, Oranee Srichaiyapol, Pornsuda Maraming, Patcharee Boonsiri, Jureerut Daduang

Survival analysis and life expectancy of pediatric patients with spinal muscular atrophy in Thailand

泰国脊髓性肌萎缩症患儿的生存分析和预期寿命

Sittiyuno, Piyanart; Kulsirichawaroj, Pimchanok; Leelahavarong, Pattara; Sanmaneechai, Oranee

Andrographolide stabilized-silver nanoparticles overcome ceftazidime-resistant Burkholderia pseudomallei: study of antimicrobial activity and mode of action

穿心莲内酯稳定的银纳米粒子克服头孢他啶耐药性伯克霍尔德菌:抗菌活性和作用方式的研究

Saengrawee Thammawithan, Chanon Talodthaisong, Oranee Srichaiyapol, Rina Patramanon, James Andell Hutchison, Sirinan Kulchat

AFM Study of Nanoscale Membrane Perturbation Induced by Antimicrobial Lipopeptide C(14) KYR

利用原子力显微镜研究抗菌脂肽C(14)KYR诱导的纳米尺度膜扰动

Nasompag, Sawinee; Siritongsuk, Pawinee; Thammawithan, Saengrawee; Srichaiyapol, Oranee; Prangkio, Panchika; Camesano, Terri A; Sinthuvanich, Chomdao; Patramanon, Rina