日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Beyond Trikafta: new models to assess tissue dependent rescue of N1303K-CFTR

Trikafta 之外:评估 N1303K-CFTR 组织依赖性拯救的新模型

Pranke, Iwona; Capurro, Valeria; Chevalier, Benoit; Pesce, Emanuela; Tomati, Valeria; Pastorino, Cristina; Kelly-Aubert, Mairead; Hatton, Aurelie; Dreano, Elise; Lena, Mariateresa; Bocciardi, Renata; Zara, Federico; Pantano, Stefano; Terlizzi, Vito; Lucanto, Cristina; Costa, Stefano; Claut, Laura; Daccò, Valeria; Poli, Piercarlo; Maschio, Massimo; Fabrizzi, Benedetta; Caporelli, Nicole; Cipolli, Marco; Volpi, Sonia; Chedevergne, Frederique; Cosson, Laure; Macey, Julie; Ramel, Sophie; Weiss, Laurence; Grenet, Dominique; Le Clainche-Viala, Laurence; Douvry, Benoit; Ravoninjatovo, Bruno; Audousset, Camille; Tatopoulos, Aurélie; Richaud-Thiriez, Bénédicte; Baravalle, Melissa; Thouvenin, Guillaume; Labbé, Guillaume; Mittaine, Marie; Reix, Philippe; Durieu, Isabelle; Mankikian, Julie; Bui, Stéphanie; Nguyen-Khoa, Thao; Khoukh, Karim; Martin, Clémence; Da Silva, Jennifer; De Carli, Paola; Castellani, Carlo; Cresta, Federico; Galietta, Luis; Guillemaut, Anne; Girodon, Emmanuelle; Remus, Natacha; Bulcaen, Mathis; Ensinck, Marjolein; Zajac, Miroslaw; Carlon, Marianne; LeBihan, Jean; Burgel, Pierre-Régis; Sermet-Gaudelus, Isabelle; Hinzpeter, Alexandre; Pedemonte, Nicoletta

The apical mucus layer alters the pharmacological properties of the airway epithelium.

顶端粘液层改变了气道上皮的药理特性

Guidone Daniela, de Santis Martina, Pesce Emanuela, Capurro Valeria, Pedemonte Nicoletta, Galietta Luis J V

Deleterious effect of Pseudomonas aeruginosa on F508del-CFTR rescued by elexacaftor/tezacaftor/ivacaftor is clinical strain-dependent in patient-derived nasal cells

铜绿假单胞菌对F508del-CFTR的有害影响(可通过elexacaftor/tezacaftor/ivacaftor挽救)在患者鼻细胞中具有临床菌株依赖性。

Allegretta, Caterina; Montemitro, Enza; Sgobba, Maria Noemi; Capurro, Valeria; Pesce, Emanuela; Ciciriello, Fabiana; La Bella, Gianfranco; Rossito, Martina; Tuccio, Vanessa; Arena, Fabio; Gunawardena, Tarini N A; Guerra, Lorenzo; Pedemonte, Nicoletta; Capitanio, Nazzareno; Piccoli, Claudia; Laselva, Onofrio

Alternative splicing and residual function potentially expand the therapeutic landscape of the CFTRdele2ins182 variant

选择性剪接和残余功能可能拓展CFTRdele2ins182变异体的治疗前景。

Pastorino, Cristina; Menta, Ludovica; Pesce, Emanuela; Lena, Mariateresa; Tomati, Valeria; Capurro, Valeria; Di Duca, Marco; Terlizzi, Vito; Gramegna, Andrea; Blasi, Francesco; Castellani, Carlo; Cappato, Serena; Zara, Federico; Pedemonte, Nicoletta; Bocciardi, Renata

Investigation of CFTR Function in Human Nasal Epithelial Cells Informs Personalized Medicine

对人鼻上皮细胞中CFTR功能的研究为个体化医疗提供信息

Pion, Audrey; Kavanagh, Erin; Joynt, Anya T; Raraigh, Karen S; Vanscoy, Lori; Langfelder-Schwind, Elinor; McNamara, John; Moore, Brooke; Patel, Shivani; Merlo, Kate; Temme, Renee; Capurro, Valeria; Pesce, Emanuela; Merlo, Christian; Pedemonte, Nicoletta; Cutting, Garry R; Sharma, Neeraj

Identification of a novel cord blood NK cell subpopulation expressing functional programmed death receptor-1

鉴定出一种表达功能性程序性死亡受体-1 的新型脐带血 NK 细胞亚群

Marco Greppi, Valentina Obino, Rayan Goda, Federico Rebaudi, Simona Carlomagno, Mariella Della Chiesa, Simona Sivori, Gianluca Ubezio, Vanessa Agostini, Alessandra Bo, Silvia Pesce, Emanuela Marcenaro

Venetoclax Shows Low Therapeutic Activity in BCL2-Positive Relapsed/Refractory Peripheral T-Cell Lymphoma: A Phase 2 Study of the Fondazione Italiana Linfomi

Venetoclax 在 BCL2 阳性复发/难治性外周 T 细胞淋巴瘤中疗效不佳:一项由意大利淋巴瘤基金会开展的 II 期研究

Ballotta, Laura; Zinzani, Pier Luigi; Pileri, Stefano; Bruna, Riccardo; Tani, Monica; Casadei, Beatrice; Tabanelli, Valentina; Volpetti, Stefano; Luminari, Stefano; Corradini, Paolo; Lucchini, Elisa; Tisi, Maria Chiara; Merli, Michele; Re, Alessandro; Varettoni, Marzia; Pesce, Emanuela Anna; Zaja, Francesco

Incidence and outcomes of rare T cell lymphomas from the T Cell Project: hepatosplenic, enteropathy associated and peripheral gamma delta T cell lymphomas

细胞项目罕见 T 细胞淋巴瘤的发病率和预后:肝脾淋巴瘤、肠病相关性淋巴瘤和外周 γδ T 细胞淋巴瘤

Foss, Francine M; Horwitz, Steven M; Civallero, Monica; Bellei, Monica; Marcheselli, Luigi; Kim, Won Seog; Cabrera, Maria E; Dlouhy, Ivan; Nagler, Arnon; Advani, Ranjana H; Pesce, Emanuela A; Ko, Young-Hyeh; Montoto, Silvia; Chiattone, Carlos; Moskowitz, Alison; Spina, Michele; Cesaretti, Marina; Biasoli, Irene; Federico, Massimo

Identification, Structure-Activity Relationship, and Biological Characterization of 2,3,4,5-Tetrahydro-1H-pyrido[4,3-b]indoles as a Novel Class of CFTR Potentiators

2,3,4,5-四氢-1H-吡啶并[4,3-b]吲哚类化合物作为一类新型CFTR增强剂的鉴定、构效关系及生物学特性研究

Brindani, Nicoletta; Gianotti, Ambra; Giovani, Simone; Giacomina, Francesca; Di Fruscia, Paolo; Sorana, Federico; Bertozzi, Sine Mandrup; Ottonello, Giuliana; Goldoni, Luca; Penna, Ilaria; Russo, Debora; Summa, Maria; Bertorelli, Rosalia; Ferrera, Loretta; Pesce, Emanuela; Sondo, Elvira; Galietta, Luis J V; Bandiera, Tiziano; Pedemonte, Nicoletta; Bertozzi, Fabio

Distinctive lipid signatures of bronchial epithelial cells associated with cystic fibrosis drugs, including Trikafta

与囊性纤维化药物(包括Trikafta)相关的支气管上皮细胞的独特脂质特征

Liessi, Nara; Pesce, Emanuela; Braccia, Clarissa; Bertozzi, Sine Mandrup; Giraudo, Alessandro; Bandiera, Tiziano; Pedemonte, Nicoletta; Armirotti, Andrea