日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Beyond Trikafta: new models to assess tissue dependent rescue of N1303K-CFTR

Trikafta 之外:评估 N1303K-CFTR 组织依赖性拯救的新模型

Pranke, Iwona; Capurro, Valeria; Chevalier, Benoit; Pesce, Emanuela; Tomati, Valeria; Pastorino, Cristina; Kelly-Aubert, Mairead; Hatton, Aurelie; Dreano, Elise; Lena, Mariateresa; Bocciardi, Renata; Zara, Federico; Pantano, Stefano; Terlizzi, Vito; Lucanto, Cristina; Costa, Stefano; Claut, Laura; Daccò, Valeria; Poli, Piercarlo; Maschio, Massimo; Fabrizzi, Benedetta; Caporelli, Nicole; Cipolli, Marco; Volpi, Sonia; Chedevergne, Frederique; Cosson, Laure; Macey, Julie; Ramel, Sophie; Weiss, Laurence; Grenet, Dominique; Le Clainche-Viala, Laurence; Douvry, Benoit; Ravoninjatovo, Bruno; Audousset, Camille; Tatopoulos, Aurélie; Richaud-Thiriez, Bénédicte; Baravalle, Melissa; Thouvenin, Guillaume; Labbé, Guillaume; Mittaine, Marie; Reix, Philippe; Durieu, Isabelle; Mankikian, Julie; Bui, Stéphanie; Nguyen-Khoa, Thao; Khoukh, Karim; Martin, Clémence; Da Silva, Jennifer; De Carli, Paola; Castellani, Carlo; Cresta, Federico; Galietta, Luis; Guillemaut, Anne; Girodon, Emmanuelle; Remus, Natacha; Bulcaen, Mathis; Ensinck, Marjolein; Zajac, Miroslaw; Carlon, Marianne; LeBihan, Jean; Burgel, Pierre-Régis; Sermet-Gaudelus, Isabelle; Hinzpeter, Alexandre; Pedemonte, Nicoletta

Adenine base editing with engineered virus-like particles rescues the CFTR mutation G542X in patient-derived intestinal organoids

利用工程改造的病毒样颗粒进行腺嘌呤碱基编辑,可挽救患者来源的肠道类器官中的 CFTR 突变 G542X。

Lucia Nicosia,Iwona Pranke,Roberta V Latorre,Joss B Murray,Lisa Lonetti,Kader Cavusoglu-Doran,Elise Dreano,James P Costello,Michael Carroll,Paola Melotti,Claudio Sorio,Isabelle Sermet-Gaudelus,Martina F Scallan,Patrick T Harrison

Galantamine-loaded PLGA nanoparticles reduce oxidative stress and inflammation in a rat model of spinal cord injury

载有加兰他敏的PLGA纳米颗粒可降低大鼠脊髓损伤模型中的氧化应激和炎症反应。

Stapenhorst Franca, Fernanda; Sperling, Laura Elena; Dos Santos, Marcelo Garrido; Teixeira, Cristian Euzebio; de Oliveira, Tiago Franco; Turck, Patrick; Klein, Adriane Bello; Pranke, Patricia

A small molecule chaperone rescues keratin-8 mediated trafficking of misfolded podocin to correct genetic Nephrotic Syndrome

小分子伴侣挽救角蛋白 8 介导的错误折叠足蛋白运输,以纠正遗传性肾病综合征

Valeryia Kuzmuk, Iwona Pranke, Ruth Rollason, Matthew Butler, Wen Y Ding, Matthew Beesley, Aoife M Waters, Richard J Coward, Richard Sessions, Jack Tuffin, Rebecca R Foster, Géraldine Mollet, Corinne Antignac, Aleksander Edelman, Gavin I Welsh, Moin A Saleem

Novel gain-of-function mutants identify a critical region within CFTR membrane-spanning domain 2 controlling cAMP-dependent and ATP-independent channel activation

新的获得功能突变体识别出 CFTR 跨膜结构域 2 内控制 cAMP 依赖性和非 ATP 依赖性通道激活的关键区域

Solène Castanier #, Ahmad Elbahnsi #, Benoit Chevalier, Nesrine Baatallah, Iwona Pranke, Lynda Berri, Aleksander Edelman, Isabelle Sermet-Gaudelus, Jean-Paul Mornon, Isabelle Callebaut #, Alexandre Hinzpeter #

Evaluation of the patency rate and endothelialization of a poly-ε-caprolactone, nanofiber sheet-based vascular graft using a rat abdominal aortic implantation model

使用大鼠腹主动脉植入模型评估聚ε-己内酯纳米纤维片基血管移植物的通畅率和内皮化

Yuta Kikuchi #, Naohiro Wakabayashi #, Daikelly I Braghirolli, Patricia Pranke, Hiroyuki Kamiya, Kyohei Oyama

Putting bicarbonate on the spot: pharmacological insights for CFTR correction in the airway epithelium

碳酸氢盐直达病灶:气道上皮中CFTR校正的药理学见解

Zajac, Miroslaw; Lepissier, Agathe; Dréano, Elise; Chevalier, Benoit; Hatton, Aurélie; Kelly-Aubert, Mairead; Guidone, Daniela; Planelles, Gabrielle; Edelman, Aleksander; Girodon, Emmanuelle; Hinzpeter, Alexandre; Crambert, Gilles; Pranke, Iwona; Galietta, Luis J V; Sermet-Gaudelus, Isabelle

Easy-to-Assembly System for Decellularization and Recellularization of Liver Grafts in a Bioreactor

用于生物反应器中肝移植片脱细胞和再细胞化的易于组装系统

Borges, Maurício Felisberto; Maurmann, Natasha; Pranke, Patricia

Keratin 8 is a scaffolding and regulatory protein of ERAD complexes

角蛋白 8 是 ERAD 复合物的支架和调节蛋白

Iwona Maria Pranke, Benoit Chevalier #, Aiswarya Premchandar #, Nesrine Baatallah, Kamil F Tomaszewski, Sara Bitam, Danielle Tondelier, Anita Golec, Jan Stolk, Gergely L Lukacs, Pieter S Hiemstra, Michal Dadlez, David A Lomas, James A Irving, Agnes Delaunay-Moisan, Eelco van Anken, Alexandre Hinzpet

Pharmacological chaperone-rescued cystic fibrosis CFTR-F508del mutant overcomes PRAF2-gated access to endoplasmic reticulum exit sites

药理学伴侣蛋白挽救的囊性纤维化 CFTR-F508del 突变体克服了 PRAF2 门控的内质网出口位点。

Kusumika Saha,Benoit Chevalier,Stéphane Doly,Nesrine Baatallah,Thomas Guilbert,Iwona Pranke,Mark G H Scott,Hervé Enslen,Chiara Guerrera,Cérina Chuon,Aleksander Edelman,Isabelle Sermet-Gaudelus ,Alexandre Hinzpeter #,Stefano Marullo #