日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Gradient nanofiber aerogels for extreme cryogenic and thermal environments

用于极端低温和高温环境的梯度纳米纤维气凝胶

Li, Chunmei; Xu, Rui; Han, Dong; Li, Puhao; Liu, Wei; Guang, Mingjian; Chao, Xujiang; Wang, Peng

Activation of endogenous full-length utrophin by MyoAAV-UA as a therapeutic approach for Duchenne muscular dystrophy.

利用 MyoAAV-UA 激活内源性全长肌营养不良蛋白作为治疗杜氏肌营养不良症的一种方法

Wu Ruo, Li Peng, Xiao Puhao, Zhang Shu, Wang Xiaopeng, Liu Jie, Sun Wenjie, Chang Yue, Ai Xiuyi, Chen Lijiao, Zhuo Yan, Wang Jiaojian, Wang Zhengbo, Li Shangang, Li Yuanyuan, Ji Weizhi, Guo Wenting, Wu Shiwen, Chen Yongchang

Single-cut gene therapy in a one-step generated rhesus monkey model of Duchenne muscular dystrophy

在一步构建的恒河猴杜氏肌营养不良症模型中进行单次基因治疗

Raoxian Bai,Wenting Guo,Ting Zhang,Shuaiwei Ren,Jie Liu,Puhao Xiao,Junyu Zhang,Wenjie Sun,Jiao Yang,Yue Ma,Siyu Liu,Chaoran Zhou,Shangang Li,Hong Wang,Shu Zhang,Weizhi Ji,Shiwen Wu,Yongchang Chen

Extensive humoral immune response to AAVs and Cas proteins in nonhuman primates

非人类灵长类动物对 AAV 和 Cas 蛋白的广泛体液免疫反应

Puhao Xiao, Raoxian Bai, Ting Zhang, Ruo Wu, Lijiao Chen, Yu Hou, Bin Shen, Yuyu Niu, Shangang Li, Weizhi Ji, Yongchang Chen

No off-target mutations in functional genome regions of a CRISPR/Cas9-generated monkey model of muscular dystrophy

在CRISPR/Cas9技术构建的肌营养不良猴模型的功能基因组区域中未发现脱靶突变

Wang, Shuang; Ren, Shuaiwei; Bai, Raoxian; Xiao, Puhao; Zhou, Qin; Zhou, Yin; Zhou, Zhigang; Niu, Yuyu; Ji, Weizhi; Chen, Yongchang