Global functional genomics reveals GRK5 as a cystic fibrosis therapeutic target synergistic with current modulators.
全球功能基因组学揭示 GRK5 是囊性纤维化治疗靶点,可与现有调节剂产生协同作用
期刊:iScience
影响因子:4.1
doi:10.1016/j.isci.2025.111942
Botelho Hugo M, Lopes-Pacheco Miquéias, Pinto Madalena C, Railean Violeta, Pankonien Ines, Caleiro Mariana F, Clarke Luka A, Cachatra Vasco, Neumann Beate, Tischer Christian, Moiteiro Cristina, Ousingsawat Jiraporn, Kunzelmann Karl, Pepperkok Rainer, Amaral Margarida D