日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Receptor-guided AAV Tropism Engineering via MATCH

通过 MATCH 技术进行受体引导的 AAV 嗜性工程

Graham, Nolan; Kumar, Satheesh; Rainaldi, Joseph; Yang, Seoin; Portell, Andrew; Santoso, Billy; Mali, Prashant

Robust genome and cell engineering via in vitro and in situ circularized RNAs

利用体外和原位环状RNA进行稳健的基因组和细胞工程

Michael Tong ,Nathan Palmer ,Amir Dailamy ,Aditya Kumar ,Hammza Khaliq ,Sangwoo Han ,Emma Finburgh ,Madeleine Wing ,Camilla Hong ,Yichen Xiang ,Katelyn Miyasaki ,Andrew Portell ,Joseph Rainaldi ,Amanda Suhardjo ,Sami Nourreddine ,Wei Leong Chew ,Ester J Kwon ,Prashant Mali

Fast growth and high-titer bioproduction from renewable formate via metal-dependent formate dehydrogenase in Escherichia coli

利用大肠杆菌中金属依赖性甲酸脱氢酶,以可再生甲酸为原料,实现快速生长和高滴度生物生产。

Cowan, Aidan E; Hillers, Mason; Rainaldi, Vittorio; Collas, Florent; Choudhary, Hemant; Zakaria, Basem S; Bieberach, Gregory G; Carruthers, David N; Grabovac, Maxwell; Gin, Jennifer W; Cawthon, Bridgie; Chen, Yan; Turumtay, Emine Akyuz; Baidoo, Edward E K; Petzold, Christopher J; Feist, Adam M; Tejedor-Sanz, Sara; Kensy, Frank; Simmons, Blake A; Keasling, Jay D; Claassens, Nico J

An engineered U7 small nuclear RNA scaffold greatly increases ADAR-mediated programmable RNA base editing

经过改造的U7小核RNA支架显著增强了ADAR介导的可编程RNA碱基编辑

Byrne, Susan M; Burleigh, Stephen M; Fragoza, Robert; Jiang, Yue; Savva, Yiannis; Pabon, Ricky; Kania, Evan; Rainaldi, Joseph; Portell, Andrew; Mali, Prashant; Briggs, Adrian W

Design and implementation of aerobic and ambient CO(2)-reduction as an entry-point for enhanced carbon fixation.

设计和实施好氧和环境 CO(2) 还原作为增强碳固定的切入点

Satanowski Ari, Marchal Daniel G, Perret Alain, Petit Jean-Louis, Bouzon Madeleine, Döring Volker, Dubois Ivan, He Hai, Smith Edward N, Pellouin Virginie, Petri Henrik M, Rainaldi Vittorio, Nattermann Maren, Burgener Simon, Paczia Nicole, Zarzycki Jan, Heinemann Matthias, Bar-Even Arren, Erb Tobias J

E. Coli cytotoxic necrotizing factor-1 promotes colorectal carcinogenesis by causing oxidative stress, DNA damage and intestinal permeability alteration

大肠杆菌细胞毒性坏死因子-1通过引起氧化应激、DNA损伤和肠道通透性改变促进结直肠癌变

Michela Tozzi #, Alessia Fiore #, Sara Travaglione, Francesca Marcon, Gabriella Rainaldi, Elena Angela Pia Germinario, Ilenia Laterza, Simona Donati, Daniele Macchia, Massimo Spada, Omar Leoni, Maria Cristina Quattrini, Donatella Pietraforte, Sofia Tomasoni, Filippo Torrigiani, Ranieri Verin, Paola

Emerging clinical applications of ADAR based RNA editing

基于ADAR的RNA编辑技术的新兴临床应用

Rainaldi, Joseph; Mali, Prashant; Nourreddine, Sami

Transplantation of Wild-Type Hematopoietic Stem and Progenitor Cells Improves Disease Phenotypes in a Mucopolysaccharidosis IIIC Mouse Model.

移植野生型造血干细胞和祖细胞可改善粘多糖贮积症 IIIC 小鼠模型的疾病表型

Badell-Grau Rafael A, Pakravesh Kasra, Thai Kevin Eric, Son Frankie, Chen Rola, Rainaldi Joseph, Duong Kalvin, Losay Pauline, Sivakumar Anusha, Khare Veenita, Corl Alexis N, Pithia Rushil, Tran Christine, Esko Jefferey D, Cherqui Stephanie

Multiplexed Pan Soluble Ligandome Assaying via OASIS

通过 OASIS 进行多重泛可溶性配体组分析

Lee, Yi-Hung; Doctor, Yesh; Zhang, Yifan; Kumar, Satheesh; Rainaldi, Joseph; Pan, Emily; Mali, Prashant

Charting and probing the activity of ADARs in human development and cell-fate specification

绘制并探究ADARs在人类发育和细胞命运决定中的活性。

Dailamy, Amir; Lyu, Weiqi; Nourreddine, Sami; Tong, Michael; Rainaldi, Joseph; McDonald, Daniella; Panwala, Rebecca; Muotri, Alysson; Breen, Michael S; Zhang, Kun; Mali, Prashant