日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

CRISPR screens in iPSC-derived neurons reveal principles of tau proteostasis.

利用 iPSC 衍生神经元进行 CRISPR 筛选揭示了 tau 蛋白稳态的原理。

Samelson Avi J, Ariqat Nabeela, McKetney Justin, Rohanitazangi Gita, Parra Bravo Celeste, Bose Rudra S, Travaglini Kyle J, Lam Victor L, Goodness Darrin, Ta Thomas, Dixon Gary, Marzette Emily, Jin Julianne, Tian Ruilin, Tse Eric, Abskharon Romany, Pan Henry S, Carroll Emma C, Lawrence Rosalie E, Gestwicki Jason E, Rexach Jessica E, Eisenberg David S, Kanaan Nicholas M, Southworth Daniel R, Gross John D, Gan Li, Swaney Danielle L, Kampmann Martin

Real-world outcomes of delandistrogene moxeparvovec gene therapy: Motor outcomes and emerging safety concerns

delandistrogene moxeparvovec 基因疗法的真实世界结果:运动功能结果和新出现的安全性问题

Keselman, Dennis J; Small, Juliana C; Seneviratne, Tiffany; McCague, Sarah; Kaschak, Taylor L; Yum, Sabrina W; O'Brien, Andrea; Brandsema, John F; Diamond, Tamir; Loomes, Kathleen M; Lin, Kimberly Y; Wittlieb-Weber, Carol A; Mayer, Oscar H; Daniel, Scott G; Waldman, Amy T; Samelson-Jones, Benjamin J; Matesanz, Susan E; George, Lindsey A

Use of CD19-targeted immune modulation to eradicate AAV-neutralizing antibodies.

利用 CD19 靶向免疫调节来根除 AAV 中和抗体

Doshi Bhavya S, Markmann Caroline A, Novak Noelle, Juarez Rojas Silvia, Davidson Robert, Chau Julia Q, Wang Wei, Carrig Sean, Martos Rus Cristina, Samelson-Jones Benjamin J, Small Juliana C, Bhoj Vijay G, George Lindsey A

Loss of factor VIII in zebrafish rebalances antithrombin deficiency but has a limited bleeding diathesis

斑马鱼体内因子VIII的缺失可以重新平衡抗凝血酶缺乏症,但出血倾向有限。

Raghunath, Azhwar; Richter, Catherine E; Griffin, Megan S; Emly, Sylvia M; Yaman, Murat; Arruda, Valder R; Samelson-Jones, Benjamin J; Shavit, Jordan A

Ex vivo lentiviral gene therapy for severe hemophilia A: an alternative to recombinant adeno-associated viral-based strategies?

体外慢病毒基因疗法治疗重度血友病A:一种替代重组腺相关病毒疗法的方案?

Samelson-Jones, Benjamin J

Initial Analysis of the Effectiveness of Compass-Behavioral for Autistic Youth: A Community-Based Retrospective Analysis

对Compass行为疗法在自闭症青少年中有效性的初步分析:一项基于社区的回顾性分析

Samelson, Doreen; Ikola, Jennifer; Fitchett, Brianna; Befi, Michelle; Bemmel, Vincent; Pfingston, Ben; Sneed, Lindsey

Purification and characterization of full-length monomeric TEC family kinase, ITK.

全长单体TEC家族激酶ITK的纯化和表征

Rathnayake Udumbara M, Wada Junya, Wall Vanessa E, Jones Jane, Jenkins Lisa M, Andreotti Amy H, Samelson Lawrence E

Ancient origin of the furin sequence in the wolf F8 gene

狼F8基因中弗林蛋白酶序列的古老起源

Siner, Joshua I; Barber-Meyer, Shannon; Samelson-Jones, Benjamin J; Mech, Lucyan David; Arruda, Valder R; Crudele, Julie M

Coagulation factor VIII: biological basis of emerging hemophilia A therapies

凝血因子VIII:新兴血友病A疗法的生物学基础

Samelson-Jones, Benjamin J; Doshi, Bhavya S; George, Lindsey A

Enhanced procoagulant activity of select hemophilia B causing factor IX variants with emicizumab

艾美赛珠单抗可增强某些导致B型血友病的IX因子变异体的促凝血活性

Lee, Kyumin; Chau, Julia Q; Suber, Yani B; Sternberg, Anna R; Pishko, Allyson M; George, Lindsey A; Bhoj, Vijay G; Doshi, Bhavya S; Samelson-Jones, Benjamin J