日期 影响因子
日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:
–

Real-world outcomes of delandistrogene moxeparvovec gene therapy: Motor outcomes and emerging safety concerns

delandistrogene moxeparvovec 基因疗法的真实世界结果：运动功能结果和新出现的安全性问题

期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2025.10.007
Keselman, Dennis J; Small, Juliana C; Seneviratne, Tiffany; McCague, Sarah; Kaschak, Taylor L; Yum, Sabrina W; O'Brien, Andrea; Brandsema, John F; Diamond, Tamir; Loomes, Kathleen M; Lin, Kimberly Y; Wittlieb-Weber, Carol A; Mayer, Oscar H; Daniel, Scott G; Waldman, Amy T; Samelson-Jones, Benjamin J; Matesanz, Susan E; George, Lindsey A
发表日期：2026
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Use of CD19-targeted immune modulation to eradicate AAV-neutralizing antibodies.

利用 CD19 靶向免疫调节来根除 AAV 中和抗体

期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2025.03.003
Doshi Bhavya S, Markmann Caroline A, Novak Noelle, Juarez Rojas Silvia, Davidson Robert, Chau Julia Q, Wang Wei, Carrig Sean, Martos Rus Cristina, Samelson-Jones Benjamin J, Small Juliana C, Bhoj Vijay G, George Lindsey A
其它
发表日期：2025
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Loss of factor VIII in zebrafish rebalances antithrombin deficiency but has a limited bleeding diathesis

斑马鱼体内因子VIII的缺失可以重新平衡抗凝血酶缺乏症，但出血倾向有限。

期刊:Blood Advances
影响因子:7.1
doi:10.1182/bloodadvances.2024013143
Raghunath, Azhwar; Richter, Catherine E; Griffin, Megan S; Emly, Sylvia M; Yaman, Murat; Arruda, Valder R; Samelson-Jones, Benjamin J; Shavit, Jordan A
发表日期：2025
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Ex vivo lentiviral gene therapy for severe hemophilia A: an alternative to recombinant adeno-associated viral-based strategies?

体外慢病毒基因疗法治疗重度血友病A：一种替代重组腺相关病毒疗法的方案？

期刊:Research and Practice in Thrombosis and Haemostasis
影响因子:3.4
doi:10.1016/j.rpth.2025.102716
Samelson-Jones, Benjamin J
微生物学
发表日期：2025
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Ancient origin of the furin sequence in the wolf F8 gene

狼F8基因中弗林蛋白酶序列的古老起源

期刊:Open Veterinary Journal
影响因子:1
doi:10.5455/OVJ.2025.v15.i7.32
Siner, Joshua I; Barber-Meyer, Shannon; Samelson-Jones, Benjamin J; Mech, Lucyan David; Arruda, Valder R; Crudele, Julie M
发表日期：2025
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Coagulation factor VIII: biological basis of emerging hemophilia A therapies

凝血因子VIII：新兴血友病A疗法的生物学基础

期刊:Blood
影响因子:23.1
doi:10.1182/blood.2023023275
Samelson-Jones, Benjamin J; Doshi, Bhavya S; George, Lindsey A
发表日期：2024
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Enhanced procoagulant activity of select hemophilia B causing factor IX variants with emicizumab

艾美赛珠单抗可增强某些导致B型血友病的IX因子变异体的促凝血活性

期刊:Blood
影响因子:23.1
doi:10.1182/blood.2023021944
Lee, Kyumin; Chau, Julia Q; Suber, Yani B; Sternberg, Anna R; Pishko, Allyson M; George, Lindsey A; Bhoj, Vijay G; Doshi, Bhavya S; Samelson-Jones, Benjamin J
发表日期：2024
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Immune tolerance induction by hepatic gene transfer: First-in-human evidence

肝脏基因转移诱导免疫耐受：首个人体证据

期刊:Molecular Therapy
影响因子:12
doi:10.1016/j.ymthe.2024.03.016
Kaczmarek, Radoslaw; Samelson-Jones, Benjamin J; Herzog, Roland W
免疫/内分泌
发表日期：2024
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Roctavian gene therapy for hemophilia A

罗克塔维亚基因疗法治疗血友病A

期刊:Blood Advances
影响因子:7.1
doi:10.1182/bloodadvances.2023011847
Samelson-Jones, Benjamin J; Small, Juliana C; George, Lindsey A
发表日期：2024
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A Novel Murine Model Enabling rAAV8-PC Gene Therapy for Severe Protein C Deficiency

一种新型小鼠模型可用于rAAV8-PC基因治疗严重蛋白C缺乏症

期刊:International Journal of Molecular Sciences
影响因子:4.9
doi:10.3390/ijms251910336
Levy-Mendelovich, Sarina; Avishai, Einat; Samelson-Jones, Benjamin J; Dardik, Rima; Brutman-Barazani, Tami; Nisgav, Yael; Livnat, Tami; Kenet, Gili
基因治疗
发表日期：2024
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