日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Durable and efficient gene silencing in vivo by hit-and-run epigenome editing

通过“命中即逃”的表观基因组编辑实现体内持久有效的基因沉默

Martino Alfredo Cappelluti, Valeria Mollica Poeta, Sara Valsoni, Piergiuseppe Quarato, Simone Merlin, Ivan Merelli, Angelo Lombardo

GP64-pseudotyped lentiviral vectors target liver endothelial cells and correct hemophilia A mice

GP64 假型慢病毒载体靶向肝内皮细胞并纠正血友病 A 小鼠

Michela Milani, Cesare Canepari, Simone Assanelli, Simone Merlin, Ester Borroni, Francesco Starinieri, Mauro Biffi, Fabio Russo, Anna Fabiano, Desirèe Zambroni, Andrea Annoni, Luigi Naldini, Antonia Follenzi, Alessio Cantore

Liver gene therapy with intein-mediated F8 trans-splicing corrects mouse haemophilia A

利用内含肽介导的 F8 反式剪接进行肝脏基因治疗可纠正小鼠血友病 A

Federica Esposito, Hristiana Lyubenova, Patrizia Tornabene, Stefano Auricchio, Antonella Iuliano, Edoardo Nusco, Simone Merlin, Cristina Olgasi, Giorgia Manni, Marco Gargaro, Francesca Fallarino, Antonia Follenzi, Alberto Auricchio

Therapeutic correction of hemophilia A by transplantation of hPSC-derived liver sinusoidal endothelial cell progenitors

通过移植 hPSC 衍生的肝窦内皮细胞祖细胞来治疗血友病 A

Blair K Gage, Simone Merlin, Cristina Olgasi, Antonia Follenzi, Gordon M Keller

Deciphering the Ets-1/2-mediated transcriptional regulation of F8 gene identifies a minimal F8 promoter for hemophilia A gene therapy

破译 Ets-1/2 介导的 F8 基因转录调控,确定用于血友病 A 基因治疗的最小 F8 启动子

Rosella Famà, Ester Borroni, Simone Merlin, Chiara Airoldi, Silvia Pignani, Alessia Cucci, Davide Corà, Valentina Bruscaggin, Sharon Scardellato, Stefania Faletti, Giuliana Pelicci, Mirko Pinotti, Gillian E Walker, Antonia Follenzi

Patient-Specific iPSC-Derived Endothelial Cells Provide Long-Term Phenotypic Correction of Hemophilia A

患者特异性 iPSC 衍生内皮细胞可对血友病 A 进行长期表型校正

Cristina Olgasi, Maria Talmon, Simone Merlin, Alessia Cucci, Yvonne Richaud-Patin, Gabriella Ranaldo, Donato Colangelo, Federica Di Scipio, Giovanni N Berta, Chiara Borsotti, Federica Valeri, Francesco Faraldi, Maria Prat, Maria Messina, Piercarla Schinco, Angelo Lombardo, Angel Raya, Antonia Follen

A Novel Platform for Immune Tolerance Induction in Hemophilia A Mice

血友病 A 小鼠免疫耐受诱导新平台

Simone Merlin, Elvira Stefania Cannizzo, Ester Borroni, Valentina Bruscaggin, Piercarla Schinco, Warut Tulalamba, Marinee K Chuah, Valder R Arruda, Thierry VandenDriessche, Maria Prat, Guido Valente, Antonia Follenzi

A long term, non-tumorigenic rat hepatocyte cell line and its malignant counterpart, as tools to study hepatocarcinogenesis

长期、非致瘤性大鼠肝细胞系及其恶性对应物,作为研究肝癌发生的工具

Maria Maddalena Angioni, Kevin Bellofatto, Simone Merlin, Silvia Menegon, Andrea Perra, Annalisa Petrelli, Pia Sulas, Silvia Giordano, Amedeo Columbano, Antonia Follenzi

The Dendritic Cell Major Histocompatibility Complex II (MHC II) Peptidome Derives from a Variety of Processing Pathways and Includes Peptides with a Broad Spectrum of HLA-DM Sensitivity

树突状细胞主要组织相容性复合体 II (MHC II) 肽组来自多种处理途径,包括具有广泛 HLA-DM 敏感性的肽

Cristina C Clement, Aniuska Becerra, Liusong Yin, Valerio Zolla, Liling Huang, Simone Merlin, Antonia Follenzi, Scott A Shaffer, Lawrence J Stern, Laura Santambrogio

Human Cardiac Progenitor Spheroids Exhibit Enhanced Engraftment Potential

人类心脏祖细胞球体表现出增强的移植潜能

Francesca Oltolina ,Andrea Zamperone ,Donato Colangelo ,Luca Gregoletto ,Simone Reano ,Stefano Pietronave ,Simone Merlin ,Maria Talmon ,Eugenio Novelli ,Marco Diena ,Carmine Nicoletti ,Antonio Musarò ,Nicoletta Filigheddu ,Antonia Follenzi ,Maria Prat