日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Engineered microRNA scaffolds for potent gene silencing in vivo.

工程化microRNA支架用于体内强效基因沉默

Militello Giuseppe, Greig Alyssa, Bi Chongfeng, Vasileva Ana, Zavodszky Maria I, Lo Shih-Ching, Guilmette Edward, Clarner Pete, Liu Bin, Bhat Guruharsha, Suh Junghae, Dow Lukas, Zuber Johannes, Fellmann Christof, Premsrirut Prem K

Inhibition of immune response reduces pathology in dorsal root ganglia and peripheral nerves in cynomolgus macaques following AAV gene therapy

抑制免疫反应可减轻食蟹猴在接受腺相关病毒(AAV)基因治疗后背根神经节和周围神经的病理变化。

Grubor, Branka; Henry, Kate L; Chan, Su Jing; Sheehan, Mark; Shah, Anumeha; Pellerin, Alex; Bai, Judy; Nadella, Prasad; Bommegowda, Santhosh; Cullen, Patrick; Tien, Eric; Chen, Vivian; van der Munnik, Nicholas P; White-Hunt, Stephanie; Plowey, Edward D; Hamann, Stefan; Guise, Amanda J; Xu, Shanqin; Kirkland, Melissa; Doherty, Jessica; Lyashenko, Eugenia; Bhat, Guruharsha; Glajch, Kelly; Lo, Shih-Ching; Gianni, Davide; Clarner, Pete; Gagnon, Jake; Chu, Jenhwa; Nambiar, Kalyani; Lulla, Mukesh; Zheng, Fengmei; Weldeab, Asmerom; Bartlett, Dan; Gutnick, Amos; Reynolds, Taylor; Zhu, Kan; Huh, Dann; Carlile, Thomas M; Fikes, James; Trapa, Patrick; Suh, Junghae; Morris, Dale; Burkly, Linda

Cis-regulatory elements driving motor neuron-selective viral payload expression within the mammalian spinal cord

驱动哺乳动物脊髓内运动神经元选择性病毒有效载荷表达的顺式调控元件

Nagy, M Aurel; Price, Spencer; Wang, Kristina; Gill, Stanley; Ren, Erika; Jayne, Lorna; Pajak, Victoria; Deighan, Sarah; Liu, Bin; Lu, Xiaodong; Diallo, Aissatou; Lo, Shih-Ching; Kleiman, Robin; Henderson, Christopher; Suh, Junghae; Griffith, Eric C; Greenberg, Michael E; Hrvatin, Sinisa

Frustration and Direct-Coupling Analyses to Predict Formation and Function of Adeno-Associated Virus

利用挫折和直接耦合分析预测腺相关病毒的形成和功能

Thadani, Nicole N; Zhou, Qin; Reyes Gamas, Kiara; Butler, Susan; Bueno, Carlos; Schafer, Nicholas P; Morcos, Faruck; Wolynes, Peter G; Suh, Junghae

Site-Specific Post-translational Surface Modification of Adeno-Associated Virus Vectors Using Leucine Zippers

利用亮氨酸拉链对腺相关病毒载体进行位点特异性翻译后表面修饰

Thadani, Nicole N; Yang, Joanna; Moyo, Buhle; Lee, Ciaran M; Chen, Maria Y; Bao, Gang; Suh, Junghae

Display of Self-Peptide on Adeno-Associated Virus Capsid Decreases Phagocytic Uptake in Vitro.

腺相关病毒衣壳上自身肽的展示会降低体外吞噬细胞的摄取

Robinson Tawana M, Chen Maria Y, Lam Michael T, Ykema Matthew R, Suh Junghae

An essential N-terminal serine-rich motif in the AAV VP1 and VP2 subunits that may play a role in viral transcription.

AAV VP1 和 VP2 亚基中一个重要的 N 端富含丝氨酸的基序可能在病毒转录中发挥作用

Robinson Tawana M, Ho Michelle L, Wahlig Brian, Gough Veronica, Banta Anton, Reyes Gamas Kiara, Kang Byunguk, Lee Esther, Chen Weitong, Suh Junghae

Protease-Activatable Adeno-Associated Virus Vector for Gene Delivery to Damaged Heart Tissue.

用于将基因递送至受损心脏组织的蛋白酶激活腺相关病毒载体

Guenther Caitlin M, Brun Mitchell J, Bennett Antonette D, Ho Michelle L, Chen Weitong, Zhu Banghe, Lam Michael, Yamagami Momona, Kwon Sunkuk, Bhattacharya Nilakshee, Sousa Duncan, Evans Annicka C, Voss Julie, Sevick-Muraca Eva M, Agbandje-McKenna Mavis, Suh Junghae

Physical, chemical, and synthetic virology: Reprogramming viruses as controllable nanodevices

物理、化学和合成病毒学:将病毒重编程为可控纳米器件

Chen, Maria Yanqing; Butler, Susan S; Chen, Weitong; Suh, Junghae

Adeno-Associated Virus (AAV) Vectors: Rational Design Strategies for Capsid Engineering

腺相关病毒(AAV)载体:衣壳工程的合理设计策略

Lee, Esther J; Guenther, Caitlin M; Suh, Junghae