日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

A compact base editor rescues AATD-associated liver and lung disease in mouse models

一种紧凑型碱基编辑器可挽救小鼠模型中与 AATD 相关的肝脏和肺部疾病

Jenny Gao; Bamidele, Nathan; Pires-Ferreira, Debora; Zheng, Chunwei; Destefano, April; Cheng, Haoyang; Tang, Qiushi; Cao, Yueying; Xie, Jun; Gao, Guangping; Gruntman, Alisha; Sontheimer, Erik; Flotte, Terence R; Xue, Wen

A Compact Base Editor Rescues AATD-associated Liver and Lung Disease in Mouse Models.

紧凑型碱基编辑器可挽救小鼠模型中与 AATD 相关的肝脏和肺部疾病

Gao Jenny, Bamidele Nathan, Pires-Ferreira Debora, Destefano April, Tang Qiushi, Cao Yueying, Xie Jun, Gao Guangping, Gruntman Alisha, Sontheimer Erik, Flotte Terence R, Xue Wen

Limb Perfusion Delivery of a rAAV1 Alpha-1 Antitrypsin Vector in Non-Human Primates Is Safe but Insufficient for Therapy

在非人灵长类动物中,通过肢体灌注递送rAAV1 α-1抗胰蛋白酶载体是安全的,但不足以用于治疗。

Pires-Ferreira, Debora; Reil, Darcy; Tang, Qiushi; Blackwood, Meghan; Gallagher, Thomas; Keeler, Allison M; Chichester, Jessica A; Vyhnal, Kristin K; Lindborg, Jane A; Benson, Janet; Fu, Dongtao; Flotte, Terence R; Gruntman, Alisha M

The application of single-cell sequencing in pancreatic neoplasm: analysis, diagnosis and treatment

单细胞测序在胰腺肿瘤中的应用:分析、诊断和治疗

Lv, Gaoyuan; Zhang, Liang; Gao, Lei; Cui, Jitao; Liu, Ziying; Sun, Bei; Wang, Gang; Tang, Qiushi

SARS-CoV-2 Serosurveys: How Antigen, Isotype and Threshold Choices Affect the Outcome

SARS-CoV-2血清学调查:抗原、同型和阈值选择如何影响结果

Binder, Raquel A; Fujimori, Gavin F; Forconi, Catherine S; Reed, George W; Silva, Leandro S; Lakshmi, Priya Saikumar; Higgins, Amanda; Cincotta, Lindsey; Dutta, Protiva; Salive, Marie-Claire; Mangolds, Virginia; Anya, Otuwe; Calvo Calle, J Mauricio; Nixon, Thomas; Tang, Qiushi; Wessolossky, Mireya; Wang, Yang; Ritacco, Dominic A; Bly, Courtney S; Fischinger, Stephanie; Atyeo, Caroline; Oluoch, Peter O; Odwar, Boaz; Bailey, Jeffrey A; Maldonado-Contreras, Ana; Haran, John P; Schmidt, Aaron G; Cavacini, Lisa; Alter, Galit; Moormann, Ann M

A nomogram for clinical estimation of acute biliary pancreatitis risk among patients with symptomatic gallstones: A retrospective case-control study

一项针对有症状胆结石患者急性胆源性胰腺炎风险的临床评估列线图:回顾性病例对照研究

Guo, Xiaoyu; Li, Yilong; Lin, Hui; Cheng, Long; Huang, Zijian; Lin, Zhitao; Mao, Ning; Sun, Bei; Wang, Gang; Tang, Qiushi

Comprehensive exploration of tumor immune microenvironment feature and therapeutic response in colorectal cancer based on a novel immune-related long non-coding RNA prognostic signature

基于新型免疫相关长链非编码RNA预后特征,全面探索结直肠癌肿瘤免疫微环境特征及治疗反应。

Zhou, Xueliang; Aikemu, Batuer; Li, Shuchun; Shao, Yanfei; Jia, Hongtao; Huang, Ling; Hong, Hiju; Zhang, Sen; Tang, Qiushi; Pan, Ruijun; Sun, Jing; Zheng, Minhua

Two-Plasmid Packaging System for Recombinant Adeno-Associated Virus.

用于重组腺相关病毒的双质粒包装系统

Tang Qiushi, Keeler Allison M, Zhang Songbo, Su Qin, Lyu Zhuoyao, Cheng Yangfan, Gao Guangping, Flotte Terence R

In Vivo Genome Editing Partially Restores Alpha1-Antitrypsin in a Murine Model of AAT Deficiency

体内基因组编辑可部分恢复AAT缺乏症小鼠模型中的α1-抗胰蛋白酶水平

Song, Chun-Qing; Wang, Dan; Jiang, Tingting; O'Connor, Kevin; Tang, Qiushi; Cai, Lingling; Li, Xiangrui; Weng, Zhiping; Yin, Hao; Gao, Guangping; Mueller, Christian; Flotte, Terence R; Xue, Wen

Sustained miRNA-mediated knockdown of mutant AAT with simultaneous augmentation of wild-type AAT has minimal effect on global liver miRNA profiles

持续的 miRNA 介导的突变型 AAT 敲低,同时增强野生型 AAT 的表达,对肝脏整体 miRNA 谱的影响甚微。

Mueller, Christian; Tang, Qiushi; Gruntman, Alisha; Blomenkamp, Keith; Teckman, Jeffery; Song, Lina; Zamore, Phillip D; Flotte, Terence R