Activation of the sigma-1 receptor chaperone alleviates symptoms of Wolfram syndrome in preclinical models
sigma-1 受体伴侣的激活可缓解临床前模型中的 Wolfram 综合征症状
期刊:Science Translational Medicine
影响因子:15.8
doi:10.1126/scitranslmed.abh3763
Lucie Crouzier, Alberto Danese, Yuko Yasui, Elodie M Richard, Jean-Charles Liévens, Simone Patergnani, Simon Couly, Camille Diez, Morgane Denus, Nicolas Cubedo, Mireille Rossel, Marc Thiry, Tsung-Ping Su, Paolo Pinton, Tangui Maurice, Benjamin Delprat