Large-scale discovery of potent, compact and erythroid specific enhancers for gene therapy vectors.
大规模发现用于基因治疗载体的高效、紧凑且红系特异性增强子
期刊:Nature Communications
影响因子:15.7
doi:10.1038/s41467-025-59235-x
Psatha Nikoletta, Sova Pavel, Georgolopoulos Grigorios, Paschoudi Kiriaki, Iwata Mineo, Bloom Jordan, Ulyanova Tatyana, Wang Hao, Kirtsou Alexandra, Vasiloudis Ninos-Ioannis, Wilken Matthew S, Stamatoyannopoulos John A, Yannaki Evangelia, Papayanopoulou Thalia, Stamatoyannopoulos George, Vierstra Jeff