Therapeutic Role of Nusinersen on Respiratory Progression in Pediatric Patients With Spinal Muscular Atrophy Type 2 and Nonambulant Type 3
Nusinersen 对 2 型和非行走型脊髓性肌萎缩症患儿呼吸系统进展的治疗作用
期刊:Neurology-Clinical Practice
影响因子:3.2
doi:10.1212/CPJ.0000000000200298
Trucco, Federica; Ridout, Deborah; Weststrate, Harriet; Scoto, Mariacristina; Rohwer, Annemarie; Coratti, Giorgia; Main, Marion L; Mayhew, Anna G; Montes, Jacqueline; De Sanctis, Roberto; Pane, Marika; Pera, Maria Carmela; Sansone, Valeria A; Albamonte, Emilio; D'Amico, Adele; Bruno, Claudio; Messina, Sonia S; Childs, Anne-Marie; Willis, Tracey; Ong, Min T; Servais, Laurent; Majumdar, Anirban; Hughes, Imelda; Marini-Bettolo, Chiara; Parasuraman, Deepak; Gowda, Vasantha L; Baranello, Giovanni; Bertini, Enrico S; De Vivo, Darryl C; Darras, Basil T; Day, John W; Mayer, Oscar; Zolkipli-Cunningham, Zarazuela; Finkel, Richard S; Mercuri, Eugenio; Muntoni, Francesco