Single-cut gene therapy in a one-step generated rhesus monkey model of Duchenne muscular dystrophy
在一步构建的恒河猴杜氏肌营养不良症模型中进行单次基因治疗
期刊:Cell Reports Medicine
影响因子:11.7
doi:10.1016/j.xcrm.2025.102037
Raoxian Bai,Wenting Guo,Ting Zhang,Shuaiwei Ren,Jie Liu,Puhao Xiao,Junyu Zhang,Wenjie Sun,Jiao Yang,Yue Ma,Siyu Liu,Chaoran Zhou,Shangang Li,Hong Wang,Shu Zhang,Weizhi Ji,Shiwen Wu,Yongchang Chen