Long-term outcomes of enzyme replacement therapy from a large cohort of Korean patients with mucopolysaccharidosis IVA (Morquio A syndrome)
韩国大量粘多糖贮积症IVA型（莫尔基奥A型综合征）患者接受酶替代疗法的长期疗效
期刊:Molecular Genetics and Metabolism Reports
影响因子:1.9
doi:10.1016/j.ymgmr.2025.101189
Sung, Juyoung; Kim, Insung; Im, Minji; Ahn, Yoon Ji; Kim, Sang-Mi; Jang, Ja-Hyun; Park, Hyung-Doo; Jeon, Tae Yeon; Ko, Kyung Rae; Park, Se-Jun; Lee, Jun Hwa; Kim, Eun Young; Cheon, Chong Kun; Kang, Eungu; Moon, Jung-Eun; Sohn, Young Bae; Lin, Hsiang-Yu; Chuang, Chih-Kuang; Lin, Shuan-Pei; Cho, Sung Yoon
