日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Liver Gene Therapy in Fabry Disease Mice With Low Doses of rAAV2/8 Expressing a Codon-Optimized hGLA cDNA Results in Long-Term Disease Correction

在法布里病小鼠模型中,使用低剂量表达密码子优化hGLA cDNA的rAAV2/8进行肝脏基因治疗可实现疾病的长期纠正。

Saxena, Himanshi; Domenis, Rossana; Romano, Giulia; Biasizzo, Jessica; Ferro, Martina; Ferino, Dania; Vicidomini, Antonio; Iaconcig, Alessandra; Bortolussi, Giulia; Zentilin, Lorena; Dardis, Andrea; Muro, Andrés F

Molecular and functional MRI enables detection of cardiac fibrosis and evaluation of treatment response after chordin-like 1 gene therapy in myocardial infarction

分子和功能磁共振成像技术能够检测心肌纤维化,并评估心肌梗死患者接受类脊索蛋白1基因治疗后的治疗反应。

Amoiradaki, Konstantina; Tomczyk, Mateusz; Wang, Xiaoying; Cruz, Gastão; Velasco, Carlos; Zentilin, Lorena; Bortolotti, Francesca; Prieto, Claudia; Botnar, René M; Giacca, Mauro; Phinikaridou, Alkystis

Cardiomyocyte SORBS2 expression increases in heart failure and regulates integrin interactions and extracellular matrix composition.

心肌细胞 SORBS2 表达在心力衰竭中增加,并调节整合素相互作用和细胞外基质组成

Timmer Louk T, den Hertog Elvira, Versteeg Danielle, Post Harm, Verdonschot Job A J, Monshouwer-Kloots Jantine, Kyriakopoulou Eirini, Perini Ilaria, Koopmans Tim, van der Kraak Petra, Zentilin Lorena, Heymans Stephane R B, Vink Aryan, Giacca Mauro, Heck Albert J R, van Rooij Eva

Living myocardial slices as a model for testing cardiac pro-reparative gene therapies.

以活体心肌切片为模型,测试心脏促修复基因疗法

Caliandro Rocco, Husetić Azra, Ligtermoet Merel L, Boender Arie R, Zentilin Lorena, Boink Gerard J J, Giacca Mauro, Gladka Monika M

Genetic tracing and topography of spontaneous and stimulated cardiac regeneration in mice.

小鼠自发性和刺激性心脏再生的遗传追踪和拓扑结构

Secco Ilaria, Backovic Ana, Tomczyk Mateusz, Mura Antonio, Li Gang, Bortolotti Francesca, Vodret Simone, Dal Ferro Matteo, Chiavacci Elena, Zentilin Lorena, Sinagra Gianfranco, Zacchigna Serena, Mano Miguel, Giacca Mauro

Spontaneous activity of astrocytes is a stochastic functional signal for memory consolidation.

星形胶质细胞的自发活动是记忆巩固的随机功能信号。

Losi Gabriele, Vignoli Beatrice, Granata Rocco, Lia Annamaria, Zonta Micaela, Sansevero Gabriele, Pischedda Francesca, Chiavegato Angela, Santi Spartaco, Zentilin Lorena, Berardi Nicoletta, Ratto Gian Michele, Carmignoto Giorgio, Canossa Marco

Delayed miR-199a Administration After Myocardial Infarction Precludes Pro-Regenerative Effects.

心肌梗死后延迟给予 miR-199a 会阻碍其促再生作用

Burjanadze Gia, Gorgodze Nikoloz, Aquaro Giovanni Donato, Gabisonia Khatia, Carlucci Lucia, Pachauri Manendra, Turreni Federico, Secco Ilaria, Bernini Fabio, Zentilin Lorena, Giacca Mauro, Recchia Fabio A

AAV6-based ZEB2 delivery promotes cardiomyocyte dedifferentiation in adult human myocardium

基于AAV6的ZEB2递送促进成人人类心肌细胞去分化

Caliandro, Rocco; Husetić, Azra; Ligtermoet, Merel L; Hanemaaijer-van der Veer, Jermo; van Duijvenboden, Karel; Zentilin, Lorena; Clerkx, Mara; Giacca, Mauro; Oostra, Roelof-Jan; van den Hoff, Maurice J B; Christoffels, Vincent M; Gladka, Monika M

EMID2 is a novel biotherapeutic for aggressive cancers identified by in vivo screening

EMID2 是一种新型生物疗法,可通过体内筛选用于治疗侵袭性癌症。

Cappelletto, Ambra; Alfì, Edoardo; Volf, Nina; Vu, Thi Van Anh; Bortolotti, Francesca; Ciucci, Giulio; Vodret, Simone; Fantuz, Marco; Perin, Martina; Colliva, Andrea; Rozzi, Giacomo; Rossi, Matilde; Ruozi, Giulia; Zentilin, Lorena; Vuerich, Roman; Borin, Daniele; Lapasin, Romano; Piazza, Silvano; Chiesa, Mattia; Lorizio, Daniela; Triboli, Luca; Kumar, Sandeep; Morello, Gaia; Tripodo, Claudio; Pinamonti, Maurizio; Piperno, Giulia Maria; Benvenuti, Federica; Rustighi, Alessandra; Jo, Hanjoong; Piccolo, Stefano; Del Sal, Giannino; Carrer, Alessandro; Giacca, Mauro; Zacchigna, Serena

Ribonucleicacid interference or small molecule inhibition of Runx1 in the border zone prevents cardiac contractile dysfunction following myocardial infarction

核糖核酸干扰或小分子抑制边界区 Runx1 可预防心肌梗死后心脏收缩功能障碍。

Martin, Tamara P; MacDonald, Eilidh A; Bradley, Ashley; Watson, Holly; Saxena, Priyanka; Rog-Zielinska, Eva A; Raheem, Anmar; Fisher, Simon; Elbassioni, Ali Ali Mohamed; Almuzaini, Ohood; Booth, Catriona; Campbell, Morna; Riddell, Alexandra; Herzyk, Pawel; Blyth, Karen; Nixon, Colin; Zentilin, Lorena; Berry, Colin; Braun, Thomas; Giacca, Mauro; McBride, Martin W; Nicklin, Stuart A; Cameron, Ewan R; Loughrey, Christopher M