Antisense-mediated exon skipping: a therapeutic strategy for titin-based dilated cardiomyopathy
反义介导的外显子跳跃:一种治疗肌联蛋白相关扩张型心肌病的策略
期刊:EMBO Molecular Medicine
影响因子:8.3
doi:10.15252/emmm.201505047
Gramlich, Michael; Pane, Luna Simona; Zhou, Qifeng; Chen, Zhifen; Murgia, Marta; Schötterl, Sonja; Goedel, Alexander; Metzger, Katja; Brade, Thomas; Parrotta, Elvira; Schaller, Martin; Gerull, Brenda; Thierfelder, Ludwig; Aartsma-Rus, Annemieke; Labeit, Siegfried; Atherton, John J; McGaughran, Julie; Harvey, Richard P; Sinnecker, Daniel; Mann, Matthias; Laugwitz, Karl-Ludwig; Gawaz, Meinrad Paul; Moretti, Alessandra