日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

CXCR2 deficiency with myelokathexis caused by a novel variant: correction via CRISPR/Cas9

由一种新型变异引起的CXCR2缺陷伴骨髓滞留:通过CRISPR/Cas9技术进行矫正

Hinke, Daniëla M; Dorset, Sofie R; Bratland, Eirik; Wolff, Jonas H; Olsnes, Astrid M; Mikkelsen, Jacob Giehm; Helgeland, Lars; Bak, Rasmus O; Benneche, Andreas; Mogensen, Trine H

Glycolytic alterations as biomarkers in polycystic kidney disease: A study using a PKD1 knockout model in NRK-52E rat kidney epithelial cells

糖酵解改变作为多囊肾病生物标志物的研究:一项利用NRK-52E大鼠肾上皮细胞PKD1基因敲除模型的研究

Mieritz, Ida Kjær; Laustsen, Christoffer; Axelgaard, Esben; Dorset, Sofie Rahbek; Bak, Rasmus O; Bertelsen, Lotte Bonde

Targeted gene editing and near-universal cDNA insertion of CYBA and CYBB as a treatment for chronic granulomatous disease

靶向基因编辑和近乎普遍的 CYBA 和 CYBB cDNA 插入作为慢性肉芽肿病的治疗方法

Wolff, Jonas Holst; Skov, Thomas Wisbech; Haslund, Didde; Dorset, Sofie Rahbek; Revenfeld, Anne Louise S; Aussel, Clotilde; Jørgensen, Sofie E; Holm, Mette; Thomsen, Martin K; Ammann, Sandra; Cathomen, Toni; Mogensen, Trine H; Møller, Bjarne Kuno; Bak, Rasmus O; Mikkelsen, Jacob Giehm

Gene editing in hematopoietic stem cells by co-delivery of Cas9/sgRNA ribonucleoprotein and templates for homology-directed repair in 'all-in-one' lentivirus-derived nanoparticles.

通过在“一体化”慢病毒衍生的纳米颗粒中共同递送 Cas9/sgRNA 核糖核蛋白和同源定向修复模板,对造血干细胞进行基因编辑

Andersen Sofie, Wolff Jonas Holst, Skov Thomas Wisbech, Janns Jacob Hørlück, Davis Luther John, Haldrup Jakob H, Haslund Didde, Revenfeld Anne Louise, Relkovic Dinko, Møller Bjarne K, Lund Jacob, Bak Rasmus O, Thomsen Emil Aagaard, Mikkelsen Jacob Giehm

Orthogonal transcriptional modulation and gene editing using multiple CRISPR-Cas systems.

利用多个 CRISPR-Cas 系统进行正交转录调控和基因编辑

Broksø Amalie Dyrelund, Bendixen Louise, Fammé Simon, Mikkelsen Kasper, Jensen Trine Ilsø, Bak Rasmus O

Single-stranded HDR templates with truncated Cas12a-binding sequences improve knock-in efficiencies in primary human T cells

带有截短的Cas12a结合序列的单链HDR模板可提高原代人T细胞的基因敲入效率

Nitulescu, Ana-Maria; Du, Weijie; Glaser, Viktor; Kath, Jonas; Aird, Eric J; Cullot, Grégoire; Greensmith, Robert; Mikkelsen, Nanna Steengaard; Stein, Maik; Bak, Rasmus O; Kaminski, Michael; Corn, Jacob E; Wagner, Dimitrios L

Corrigendum: Characterization of TLR9 responsiveness in cell subsets derived from in vitro pDC differentiation of hematopoietic stem and progenitor cells

更正:体外造血干细胞和祖细胞pDC分化衍生的细胞亚群中TLR9反应性的表征

Sánchez Hernández, Sabina; Bjerg, Tobias Wang; Helstrup Nielsen, Ian; Laustsen, Anders; Q Tang, Hai; Henning Pedersen, Lars; Klechevsky, Eynav; Jakobsen, Martin R; Bak, Rasmus O

Characterization of the role of spatial proximity of DNA double-strand breaks in the formation of CRISPR-Cas9-induced large structural variations

阐明DNA双链断裂空间邻近性在CRISPR-Cas9诱导的大结构变异形成中的作用

Dahl-Jessen, Mikkel; Terkelsen, Thorkild; Bak, Rasmus O; Jensen, Uffe Birk

Enrichment strategies to enhance genome editing

增强基因组编辑的富集策略

Mikkelsen, Nanna S; Bak, Rasmus O

CRISPR-Cas-mediated transcriptional modulation: The therapeutic promises of CRISPRa and CRISPRi

CRISPR-Cas介导的转录调控:CRISPRa和CRISPRi的治疗前景

Bendixen, Louise; Jensen, Trine I; Bak, Rasmus O