日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Virus-free CRISPR knockin of a chimeric antigen receptor into KLRC1 generates potent GD2-specific natural killer cells.

利用无病毒 CRISPR 技术将嵌合抗原受体敲入 KLRC1 中,可产生强效的 GD2 特异性自然杀伤细胞

Shankar Keerthana, Zingler-Hoslet Isabelle, Tabima Diana M, Zima Seth, Shi Lei, Gimse Kirstan, Forsberg Matthew H, Katta Varun, Davis Sage Z, Maldonado Daniel, Russell Brittany E, Murtaza Muhammed, Tsai Shengdar Q, Ayuso Jose M, Capitini Christian M, Saha Krishanu

Efficient nonviral integration of large transgenes into human T cells using Cas9-CLIPT.

利用 Cas9-CLIPT 将大型转基因高效非病毒整合到人类 T 细胞中

Tommasi Anna, Cappabianca Dan, Bugel Madison, Gimse Kirstan, Lund-Peterson Karl, Shrestha Hum, Arutyunov Denis, Williams James A, Police Seshidhar Reddy, Indurthi Venkata, Davis Sage Z, Murtaza Muhammed, Capitini Christian M, Saha Krishanu

Long term rescue of Alzheimer's deficits in vivo by one-time gene-editing of App C-terminus

通过一次性基因编辑 App C 端来长期挽救阿尔茨海默病的体内缺陷

Brent D Aulston, Kirstan Gimse, Hannah O Bazick, Eniko A Kramar, Donald P Pizzo, Leonardo A Parra-Rivas, Jichao Sun, Kristen Branes-Guerrero, Nidhi Checka, Neda Bagheri, Nihal Satyadev, Jared Carlson-Stevermer, Takashi Saito, Takaomi C Saido, Anjon Audhya, Marcelo A Wood, Mark J Zylka, Krishanu Saha

Efficient in vivo neuronal genome editing in the mouse brain using nanocapsules containing CRISPR-Cas9 ribonucleoproteins

利用含有CRISPR-Cas9核糖核蛋白的纳米胶囊在小鼠脑内进行高效的体内神经元基因组编辑

Metzger, Jeanette M; Wang, Yuyuan; Neuman, Samuel S; Snow, Kathy J; Murray, Stephen A; Lutz, Cathleen M; Bondarenko, Viktoriya; Felton, Jesi; Gimse, Kirstan; Xie, Ruosen; Li, Dongdong; Zhao, Yi; Flowers, Matthew T; Simmons, Heather A; Roy, Subhojit; Saha, Krishanu; Levine, Jon E; Emborg, Marina E; Gong, Shaoqin