日期:
2020 年 — 2026 年
2020
2021
2022
2023
2024
2025
2026
影响因子:

Z variant heterozygosity in alpha-1 antitrypsin deficiency: disease risk and treatment implications

α1-抗胰蛋白酶缺乏症中Z变异杂合性:疾病风险和治疗意义

Hersh, Craig P; Teckman, Jeffrey H; Strnad, Pavel; Hakim, Aaron; Carroll, Tomás P; Hall, Ian P; Ghosh, Auyon J; Barjaktarevic, Igor; McElvaney, Noel G; Kaserman, Joseph E; Lomas, David A; Strange, Charlie; Drummond, M Bradley; Rennard, Stephen; Hanna, Kathi E; Clark, Virginia C; Goldklang, Monica P; Iverson, Peg; Wilson, Andrew A

Thyroid hormone receptor beta (THRβ1) is the major regulator of T3 action in human iPSC-derived hepatocytes

甲状腺激素受体β(THRβ1)是人类iPSC衍生肝细胞中T3作用的主要调节因子。

Lorraine Soares De Oliveira ,Joseph E Kaserman ,Anne H Van Der Spek ,Nora J Lee ,Hendrik J Undeutsch ,Rhiannon B Werder ,Andrew A Wilson ,Anthony N Hollenberg

Disturbed function of TBL1X has a differential effect on T3-regulated gene expression in two human liver cell models

TBL1X功能紊乱对两种人肝细胞模型中T3调控的基因表达具有不同的影响

Hu, Yalan; Soares De Oliveira, Lorraine; Falize, Kim; Paul van Trotsenburg, A S; Fliers, Eric; Kaserman, Joseph E; Wilson, Andrew A; Hollenberg, Anthony N; Bruinstroop, Eveline; Boelen, Anita

Human iPSC-hepatocyte modeling of alpha-1 antitrypsin heterozygosity reveals metabolic dysregulation and cellular heterogeneity

人诱导多能干细胞-肝细胞模型揭示了α-1抗胰蛋白酶杂合性代谢紊乱和细胞异质性

Joseph E Kaserman ,Rhiannon B Werder ,Feiya Wang ,Taylor Matte ,Michelle I Higgins ,Mark Dodge ,Jonathan Lindstrom-Vautrin ,Pushpinder Bawa ,Anne Hinds ,Esther Bullitt ,Ignacio S Caballero ,Xu Shi ,Robert E Gerszten ,Nicola Brunetti-Pierri ,Marc Liesa ,Carlos Villacorta-Martin ,Anthony N Hollenberg ,Darrell N Kotton ,Andrew A Wilson

Human iPSC-hepatocyte modeling of alpha-1 antitrypsin heterozygosity reveals metabolic dysregulation and cellular heterogeneity

人诱导多能干细胞-肝细胞模型揭示了α-1抗胰蛋白酶杂合性的代谢紊乱和细胞异质性

Joseph E Kaserman,Rhiannon B Werder,Feiya Wang,Taylor Matte,Michelle I Higgins,Mark Dodge,Jonathan Lindstrom-Vautrin,Pushpinder Bawa,Anne Hinds,Esther Bullitt,Ignacio S Caballero,Xu Shi,Robert E Gerszten,Nicola Brunetti-Pierri,Marc Liesa,Carlos Villacorta-Martin,Anthony N Hollenberg,Darrell N Kotton,Andrew A Wilson

Ebola virus infection induces a delayed type I IFN response in bystander cells and the shutdown of key liver genes in human iPSC-derived hepatocytes

埃博拉病毒感染会诱发旁观者细胞中 I 型干扰素反应延迟,并导致人类 iPSC 衍生肝细胞中关键肝脏基因关闭

Whitney A Scoon, Liliana Mancio-Silva, Ellen L Suder, Carlos Villacorta-Martin, Jonathan Lindstrom-Vautrin, John G Bernbaum, Steve Mazur, Reed F Johnson, Judith Olejnik, Elizabeth Y Flores, Aditya Mithal, Feiya Wang, Adam J Hume, Joseph E Kaserman, Sandra March-Riera, Andrew A Wilson, Sangeeta N Bha

Recombinant Lloviu virus as a tool to study viral replication and host responses

重组 Lloviu 病毒作为研究病毒复制和宿主反应的工具

Adam J Hume, Baylee Heiden, Judith Olejnik, Ellen L Suder, Stephen Ross, Whitney A Scoon, Esther Bullitt, Maria Ericsson, Mitchell R White, Jacquelyn Turcinovic, Tran T N Thao, Ryan M Hekman, Joseph E Kaserman, Jessie Huang, Konstantinos-Dionysios Alysandratos, Gabor E Toth, Ferenc Jakab, Darrell N

Adenine base editing reduces misfolded protein accumulation and toxicity in alpha-1 antitrypsin deficient patient iPSC-hepatocytes

腺嘌呤碱基编辑可减少 α-1 抗胰蛋白酶缺乏症患者 iPSC 肝细胞中错误折叠蛋白质的积累和毒性

Rhiannon B Werder, Joseph E Kaserman, Michael S Packer, Jonathan Lindstrom-Vautrin, Carlos Villacorta-Martin, Lauren E Young, Yvonne Aratyn-Schaus, Francine Gregoire, Andrew A Wilson

A Highly Phenotyped Open Access Repository of Alpha-1 Antitrypsin Deficiency Pluripotent Stem Cells

高度表型化的 Alpha-1 抗胰蛋白酶缺乏症多能干细胞开放存取库

Joseph E Kaserman, Killian Hurley, Mark Dodge, Carlos Villacorta-Martin, Marall Vedaie, Jyh-Chang Jean, Derek C Liberti, Marianne F James, Michelle I Higgins, Nora J Lee, George R Washko, Raul San Jose Estepar, Jeffrey Teckman, Darrell N Kotton, Andrew A Wilson

hiPSC hepatocyte model demonstrates the role of unfolded protein response and inflammatory networks in α(1)-antitrypsin deficiency

hiPSC肝细胞模型揭示了未折叠蛋白反应和炎症网络在α(1)-抗胰蛋白酶缺乏症中的作用

Segeritz, Charis-Patricia; Rashid, Sheikh Tamir; de Brito, Miguel Cardoso; Serra, Maria Paola; Ordonez, Adriana; Morell, Carola Maria; Kaserman, Joseph E; Madrigal, Pedro; Hannan, Nicholas R F; Gatto, Laurent; Tan, Lu; Wilson, Andrew A; Lilley, Kathryn; Marciniak, Stefan J; Gooptu, Bibek; Lomas, David A; Vallier, Ludovic